相关参考文献
注意：仅列出部分参考文献，下载原文获取全部文献信息。Diagnosis and treatment trends in mucopolysaccharidosis I: findings from the MPS I Registry
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The MPS I registry: Design, methodology, and early findings of a global disease registry for monitoring patients with Mucopolysaccharidosis Type I
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A follow-up study of MPS I patients treated with laronidase enzyme replacement therapy for 6 years
Monica Sifuentes et al.
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Enzyme replacement therapy for mucopolysaccharidosis I:: A randomized, double-blinded, placebo-controlled, multinational study of recombinant human α-L-iduronidase (Laronidase)
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Enzyme-replacement therapy in mucopolysaccharidosis I.
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NEW ENGLAND JOURNAL OF MEDICINE (2001)
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