期刊
GENE THERAPY
卷 13, 期 14, 页码 1061-1067出版社
NATURE PUBLISHING GROUP
DOI: 10.1038/sj.gt.3302809
关键词
cystic fibrosis; airway gene transfer; viral vectors; non-viral vectors
Our first review on progress and prospects in cystic fibrosis ( CF) gene therapy was published in this series in October 2002. We now summarize the progress made since then and comment on the prospects for CF gene therapy over the next couple of years. Three clinical trials have been carried out, further supporting the proof-of-principle that gene transfer to the airway epithelium is feasible. Developments in viral and non-viral vectors, as well as recent alternative strategies such as gene repair, trans-splicing and stem cell therapy will be reviewed.
作者
我是这篇论文的作者
点击您的名字以认领此论文并将其添加到您的个人资料中。
推荐
暂无数据