4.2 Article

226th ENMC International Workshop: Towards validated and qualified biomarkers for therapy development for Duchenne muscular dystrophy 20-22 January 2017, Heemskerk, The Netherlands

期刊

NEUROMUSCULAR DISORDERS
卷 28, 期 1, 页码 77-86

出版社

PERGAMON-ELSEVIER SCIENCE LTD
DOI: 10.1016/j.nmd.2017.10.002

关键词

Duchenne muscular dystrophy; Biomarker; Dystrophin; MRI; Biobank

资金

  1. Association Francaise contre les Myopathies (France)
  2. Deutsche Gesellschaft fur Muskelkranke (Germany)
  3. Muscular Dystrophy Campaign (UK)
  4. Muskelsvindfonden (Denmark)
  5. Prinses Beatrix Spierfonds (The Netherlands)
  6. Schweizerische Stiftung fur die Erforschung der Muskelkrankheiten (Switzerland)
  7. Telethon Foundation (Italy)
  8. Spierziekten Nederland (The Netherlands)
  9. Finnish Neuromuscular Association (Finland)
  10. NATIONAL HEART, LUNG, AND BLOOD INSTITUTE [R01HL061322] Funding Source: NIH RePORTER
  11. NATIONAL INSTITUTE OF ARTHRITIS AND MUSCULOSKELETAL AND SKIN DISEASES [U54AR052646] Funding Source: NIH RePORTER

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