Antisense oligonucleotide drugs for Duchenne muscular dystrophy: how far have we come and what does the future hold?

FUTURE MEDICINAL CHEMISTRY

卷 7, 期 13, 页码 1631-1635

FUTURE SCI LTD

2 '-O methyl phosphorothioate antisense oligonucleotides; antisense therapy; drisapersen; Duchenne muscular dystrophy; eteplirsen; exon skipping; phosphorodiamidate morpholino oligomers; tricyclo-DNA oligomers

Chemistry, Medicinal

1. Canadian Institutes of Health Research Funding Source: Medline