期刊
NEUROMUSCULAR DISORDERS
卷 27, 期 7, 页码 693-701出版社
PERGAMON-ELSEVIER SCIENCE LTD
DOI: 10.1016/j.nmd.2017.02.013
关键词
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资金
- Foundation to Eradicate Duchenne
- AGADA BioSciences
- Biogen
- Biomarin
- Catabasis
- Lilly
- Idera
- Italfarmaco
- MDA USA
- PTC Therapeutics
- Sarepta Therapeutics