相关参考文献
注意：仅列出部分参考文献，下载原文获取全部文献信息。Bioresponsive materials
Yue Lu et al.
NATURE REVIEWS MATERIALS (2017)
LEVERAGING PHYSIOLOGY FOR PRECISION DRUG DELIVERY
Wujin Sun et al.
PHYSIOLOGICAL REVIEWS (2017)
Beyond editing: repurposing CRISPR-Cas9 for precision genome regulation and interrogation
Antonia A. Dominguez et al.
NATURE REVIEWS MOLECULAR CELL BIOLOGY (2016)
Applications of CRISPR-Cas systems in neuroscience
Matthias Heidenreich et al.
NATURE REVIEWS NEUROSCIENCE (2016)
In vivo gene editing in dystrophic mouse muscle and muscle stem cells
Mohammadsharif Tabebordbar et al.
SCIENCE (2016)
Therapeutic genome editing by combined viral and non-viral delivery of CRISPR system components in vivo
Hao Yin et al.
NATURE BIOTECHNOLOGY (2016)
Efficient delivery of genome-editing proteins using bioreducible lipid nanoparticles
Ming Wang et al.
PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA (2016)
CRISPR-Cas Gene Editing to Cure Serious Diseases: Treat the Patient, Not the Germ Line
Ante S. Lundberg et al.
AMERICAN JOURNAL OF BIOETHICS (2015)
Self-Assembled DNA Nanoclews for the Efficient Delivery of CRISPR-Cas9 for Genome Editing
Wujin Sun et al.
ANGEWANDTE CHEMIE-INTERNATIONAL EDITION (2015)
From Genomics to Gene Therapy: Induced Pluripotent Stem Cells Meet Genome Editing
Akitsu Hotta et al.
ANNUAL REVIEW OF GENETICS, VOL 49 (2015)
CRISPR genome engineering and viral gene delivery: A case of mutual attraction
Florian Schmidt et al.
BIOTECHNOLOGY JOURNAL (2015)
In vivo genome editing using Staphylococcus aureus Cas9
F. Ann Ran et al.
NATURE (2015)
CRISPR germline engineering-the community speaks
Katrine S. Bosley et al.
NATURE BIOTECHNOLOGY (2015)
A light-inducible CRISPR-Cas9 system for control of endogenous gene activation
Lauren R. Polstein et al.
NATURE CHEMICAL BIOLOGY (2015)
Delivering the goods: Scientists seek a way to make CRISPR-Cas gene editing more targeted
Amanda B. Keener
NATURE MEDICINE (2015)
Gene therapy approaches to regenerating the musculoskeletal system
Christopher H. Evans et al.
NATURE REVIEWS RHEUMATOLOGY (2015)
Genome-wide inactivation of porcine endogenous retroviruses (PERVs)
Luhan Yang et al.
SCIENCE (2015)
CRISPR/Cas9-mediated gene editing in human tripronuclear zygotes
Puping Liang et al.
PROTEIN & CELL (2015)
CRISPR genome engineering and viral gene delivery: A case of mutual attraction
Florian Schmidt et al.
BIOTECHNOLOGY JOURNAL (2015)
CRISPR-Cas9 delivery to hard-to-transfect cells via membrane deformation
Xin Han et al.
SCIENCE ADVANCES (2015)
Cationic lipid-mediated delivery of proteins enables efficient protein-based genome editing in vitro and in vivo
John A. Zuris et al.
NATURE BIOTECHNOLOGY (2015)
CRISPR-Cas9 Knockin Mice for Genome Editing and Cancer Modeling
Randall J. Platt et al.
CELL (2014)
Generation of Gene-Modified Cynomolgus Monkey via Cas9/RNA-Mediated Gene Targeting in One-Cell Embryos
Yuyu Niu et al.
CELL (2014)
Gene disruption by cell-penetrating peptide-mediated delivery of Cas9 protein and guide RNA
Suresh Ramakrishna et al.
GENOME RESEARCH (2014)
Highly efficient RNA-guided genome editing in human cells via delivery of purified Cas9 ribonucleoproteins
Sojung Kim et al.
GENOME RESEARCH (2014)
Gene Therapy Briefs
Alex Philippidis
HUMAN GENE THERAPY (2014)
Simple generation of albino C57BL/6J mice with G291T mutation in the tyrosinase gene by the CRISPR/Cas9 system
Seiya Mizuno et al.
MAMMALIAN GENOME (2014)
Genome editing with Cas9 in adult mice corrects a disease mutation and phenotype
Hao Yin et al.
NATURE BIOTECHNOLOGY (2014)
Function-based identification of mammalian enhancers using site-specific integration
Diane E. Dickel et al.
NATURE METHODS (2014)
Non-viral vectors for gene-based therapy
Hao Yin et al.
NATURE REVIEWS GENETICS (2014)
The new frontier of genome engineering with CRISPR-Cas9
Jennifer A. Doudna et al.
SCIENCE (2014)
Efficient genome engineering by targeted homologous recombination in mouse embryos using transcription activator-like effector nucleases
Daniel Sommer et al.
NATURE COMMUNICATIONS (2014)
High-frequency off-target mutagenesis induced by CRISPR-Cas nucleases in human cells
Yanfang Fu et al.
NATURE BIOTECHNOLOGY (2013)
Progress in gene therapy for neurological disorders
Michele Simonato et al.
NATURE REVIEWS NEUROLOGY (2013)
Hemophilia clinical gene therapy: brief review
Christopher E. Walsh et al.
TRANSLATIONAL RESEARCH (2013)
A Programmable Dual-RNA-Guided DNA Endonuclease in Adaptive Bacterial Immunity
Martin Jinek et al.
SCIENCE (2012)
分享论文
