期刊
SCIENCE TRANSLATIONAL MEDICINE
卷 8, 期 364, 页码 -出版社
AMER ASSOC ADVANCEMENT SCIENCE
DOI: 10.1126/scitranslmed.aal2074
关键词
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资金
- Texas Children's Hospital
- Jan and Dan Duncan Neurological Research Institute
- A-T Children's Project, Perkins+Will
- Alzheimer's Drug Discovery Foundation
- Beyond Batten Disease Foundation
- BioMarin
- Bruker
- FORUM Pharmaceuticals
- Lonza
- Lundbeck
- National Ataxia Foundation
- UCB Pharmaceuticals
- Thermo Fisher
- VWR