相关参考文献
注意:仅列出部分参考文献,下载原文获取全部文献信息。A Phase 2 study of L-asparaginase encapsulated in erythrocytes in elderly patients with Philadelphia chromosome negative acute lymphoblastic leukemia: The GRASPALL/GRAALL-SA2-2008 study
Mathilde Hunault-Berger et al.
AMERICAN JOURNAL OF HEMATOLOGY (2015)
Long-Term Prognosis of Patients with Infantile-Onset Pompe Disease Diagnosed by Newborn Screening and Treated since Birth
Yin-Hsiu Chien et al.
JOURNAL OF PEDIATRICS (2015)
Discussion about Several Potential Drawbacks of PEGylated Therapeutic Proteins
Fan Zhang et al.
BIOLOGICAL & PHARMACEUTICAL BULLETIN (2014)
Approaches to erythrocyte-mediated drug delivery
Mauro Magnani et al.
EXPERT OPINION ON DRUG DELIVERY (2014)
A multicenter open-label treatment protocol (HGT-GCB-058) of velaglucerase alfa enzyme replacement therapy in patients with Gaucher disease type 1: safety and tolerability
Gregory M. Pastores et al.
GENETICS IN MEDICINE (2014)
Erythrocyte-mediated delivery of phenylalanine ammonia lyase for the treatment of phenylketonuria in BTBR-Pahenu2 mice
Luigia Rossi et al.
JOURNAL OF CONTROLLED RELEASE (2014)
Cell-penetrating peptides meditated encapsulation of protein therapeutics into intact red blood cells and its application
Huining He et al.
JOURNAL OF CONTROLLED RELEASE (2014)
Single-dose, subcutaneous recombinant phenylalanine ammonia lyase conjugated with polyethylene glycol in adult patients with phenylketonuria: an open-label, multicentre, phase 1 dose-escalation trial
Nicola Longo et al.
LANCET (2014)
Intra-Erythrocyte Infusion of Dexamethasone Reduces Neurological Symptoms in Ataxia Teleangiectasia Patients: Results of a Phase 2 Trial
Luciana Chessa et al.
ORPHANET JOURNAL OF RARE DISEASES (2014)
Advanced drug delivery systems for antithrombotic agents
Colin F. Greineder et al.
BLOOD (2013)
Erythrocytes encapsulated with phenylalanine hydroxylase exhibit improved pharmacokinetics and lowered plasma phenylalanine levels in normal mice
Nelson S. Yew et al.
MOLECULAR GENETICS AND METABOLISM (2013)
CLINICAL AND BIOCHEMICAL IMPROVEMENTS IN A PATIENT WITH MNGIE FOLLOWING ENZYME REPLACEMENT
Bridget E. Bax et al.
NEUROLOGY (2013)
Engineering antigens for in situ erythrocyte binding induces T-cell deletion
Stephan Kontos et al.
PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA (2013)
Outcome of hematopoietic stem cell transplantation for adenosine deaminase-deficient severe combined immunodeficiency
Amel Hassan et al.
BLOOD (2012)
Efficacy of homologous inositol hexaphosphate-loaded red blood cells in sickle transgenic mice
Vanessa Bourgeaux et al.
BRITISH JOURNAL OF HAEMATOLOGY (2012)
Allogeneic hematopoietic SCT as treatment option for patients with mitochondrial neurogastrointestinal encephalomyopathy (MNGIE): a consensus conference proposal for a standardized approach
J. Halter et al.
BONE MARROW TRANSPLANTATION (2011)
Clinical and genetic spectrum of mitochondrial neurogastrointestinal encephalomyopathy
Caterina Garone et al.
BRAIN (2011)
L-asparaginase loaded red blood cells in refractory or relapsing acute lymphoblastic leukaemia in children and adults: results of the GRASPALL 2005-01 randomized trial
Carine Domenech et al.
BRITISH JOURNAL OF HAEMATOLOGY (2011)
Drug Delivery by Red Blood Cells
Sara Biagiotti et al.
IUBMB LIFE (2011)
Cognitive, neurophysiological, neurological and psychosocial outcomes in early-treated PKU-patients: A start toward standardized outcome measurement across development
F. J. van Spronsen et al.
MOLECULAR GENETICS AND METABOLISM (2011)
FDA-approved poly(ethylene glycol)-protein conjugate drugs
Steevens N. S. Alconcel et al.
POLYMER CHEMISTRY (2011)
Limited dCTP Availability Accounts for Mitochondrial DNA Depletion in Mitochondrial Neurogastrointestinal Encephalomyopathy (MNGIE)
Emiliano Gonzalez-Vioque et al.
PLOS GENETICS (2011)
Drug delivery by red blood cells: vascular carriers designed by mother nature
Vladimir R. Muzykantov
EXPERT OPINION ON DRUG DELIVERY (2010)
Delivery of Therapeutic Proteins
Dipak S. Pisal et al.
JOURNAL OF PHARMACEUTICAL SCIENCES (2010)
Targeting of a Mutant Plasminogen Activator to Circulating Red Blood Cells for Prophylactic Fibrinolysis
Sergei Zaitzev et al.
JOURNAL OF PHARMACOLOGY AND EXPERIMENTAL THERAPEUTICS (2010)
Cell-based drug delivery
F. Pierige et al.
ADVANCED DRUG DELIVERY REVIEWS (2008)
Encapsulation of glutamine synthetase in mouse erythrocytes: a new procedure for ammonia detoxification
Elena A. Kosenko et al.
BIOCHEMISTRY AND CELL BIOLOGY (2008)
Drug Loaded Erythrocytes: As Novel Drug Delivery System
R. Hirlekar et al.
CURRENT PHARMACEUTICAL DESIGN (2008)
Nano/micro technologies for delivering macromolecular therapeutics using poly(D,L-lactide-co-glycolide) and its derivatives
Raghavendra C. Mundargi et al.
JOURNAL OF CONTROLLED RELEASE (2008)
Delivery of acid sphingomyelinase in normal and Niemann-Pick disease mice using intercellular adhesion molecule-1-targeted polymer nanocarriers
Carmen Garnacho et al.
JOURNAL OF PHARMACOLOGY AND EXPERIMENTAL THERAPEUTICS (2008)
Carrier erythrocyte entrapped thymidine phosphorylas etherapy for MNGIE
N. F. Moran et al.
NEUROLOGY (2008)
A 9-yr evaluation of carrier erythrocyte encapsulated adenosine deaminase (ADA) therapy in a patient with adult-type ADA deficiency
Bridget E. Bax et al.
EUROPEAN JOURNAL OF HAEMATOLOGY (2007)
Thymidine and deoxyuridine accumulate in tissues of patients with mitochondrial neurogastrointestinal encephalomyopathy (MNGIE)
Maria Lucia Valentino et al.
FEBS LETTERS (2007)
Applications of carrier erythrocytes in delivery of biopharmaceuticals
Mehrdad Hamidi et al.
JOURNAL OF CONTROLLED RELEASE (2007)
Infusion of platelets transiently reduces nucleoside overload in MNGIE
M. C. Lara et al.
NEUROLOGY (2006)
Strategies to improve plasma half life time of peptide and protein drugs
M. Werle et al.
AMINO ACIDS (2006)
Thymidine phosphorylase gene mutations cause mitochondrial neurogastrointestinal encephalomyopathy (MNGIE)
Michio Hirano et al.
INTERNAL MEDICINE (2006)
The role of mannosylated enzyme and the mannose receptor in enzyme replacement therapy
H Du et al.
AMERICAN JOURNAL OF HUMAN GENETICS (2005)
Developmentally regulated mannose 6-phosphate receptor-mediated transport of a lysosomal enzyme across the blood-brain barrier
A Urayama et al.
PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA (2004)
Altered thymidine metabolism due to defects of thymidine phosphorylase
A Spinazzola et al.
JOURNAL OF BIOLOGICAL CHEMISTRY (2002)
Mouse erythrocytes as carriers for coencapsulated alcohol and aldehyde dehydrogenase obtained by electroporation -: In vivo survival rate in circulation, organ distribution and ethanol degradation
C Lizano et al.
LIFE SCIENCES (2001)
In vitro and in vivo studies with human carrier erythrocytes loaded with polyethylene glycol-conjugated and native adenosine deaminase
BE Bax et al.
BRITISH JOURNAL OF HAEMATOLOGY (2000)