相关参考文献
注意：仅列出部分参考文献，下载原文获取全部文献信息。A Practical Guide to the Treatment of Dravet Syndrome with Anti-Seizure Medication
Adam Strzelczyk et al.
CNS DRUGS (2022)
Guidance on Dravet syndrome from infant to adult care: Road map for treatment planning in Europe
Elena Cardenal-Munoz et al.
EPILEPSIA OPEN (2022)
Fenfluramine for Treatment-Resistant Seizures in Patients With Dravet Syndrome Receiving Stiripentol-Inclusive Regimens A Randomized Clinical Trial
Rima Nabbout et al.
JAMA NEUROLOGY (2020)
Dose-Ranging Effect of Adjunctive Oral Cannabidiol vs Placebo on Convulsive Seizure Frequency in Dravet Syndrome A Randomized Clinical Trial
Ian Miller et al.
JAMA NEUROLOGY (2020)
Efficacy and safety of Fenfluramine hydrochloride for the treatment of seizures in Dravet syndrome: A real-world study
Nicola Specchio et al.
EPILEPSIA (2020)
Fenfluramine HCl (Fintepla(R)) provides long-term clinically meaningful reduction in seizure frequency: Analysis of an ongoing open-label extension study
Joseph Sullivan et al.
EPILEPSIA (2020)
Impact of the therapeutic positioning report in the P&R process in Spain: analysis of orphan drugs approved by the European Commission and reimbursed in Spain from 2003 to 2019
Xavier Badia et al.
ORPHANET JOURNAL OF RARE DISEASES (2020)
Analysis of the family impact and needs of Dravet's syndrome in Spain
Angel Aledo-Serrano et al.
REVISTA DE NEUROLOGIA (2020)
Caregiver impact and health service use in high and low severity Dravet syndrome: A multinational cohort study
Lieven Lagae et al.
SEIZURE-EUROPEAN JOURNAL OF EPILEPSY (2019)
Development and validation of an MCDA framework for evaluation and decision-making of orphan drugs in Spain
Xavier Badia et al.
EXPERT OPINION ON ORPHAN DRUGS (2019)
Long-term cannabidiol treatment in patients with Dravet syndrome: An open-label extension trial
Orrin Devinsky et al.
EPILEPSIA (2019)
Fenfluramine hydrochloride for the treatment of seizures in Dravet syndrome: a randomised, double-blind, placebo-controlled trial
Lieven Lagae et al.
LANCET (2019)
Autism spectrum disorder and cognitive profile in children with Dravet syndrome: Delineation of a specific phenotype
Lisa Ouss et al.
EPILEPSIA OPEN (2019)
Determining the value contribution of emicizumab (Hemlibra®) for the prophylaxis of haemophilia A with inhibitors in Spain by multi-criteria decision analysis
Maria Teresa Alvarez-Roman et al.
GLOBAL & REGIONAL HEALTH TECHNOLOGY ASSESSMENT (2019)
Treatment Strategies for Dravet Syndrome
Kelly G. Knupp et al.
CNS DRUGS (2018)
Assessing the impact of caring for a child with Dravet syndrome: Results of a caregiver survey
Jonathan D. Campbell et al.
EPILEPSY & BEHAVIOR (2018)
Quality of life and comorbidities associated with Dravet syndrome severity: a multinational cohort survey
Lieven Lagae et al.
DEVELOPMENTAL MEDICINE AND CHILD NEUROLOGY (2018)
DRUG EVALUATION AND DECISION MAKING IN CATALONIA: DEVELOPMENT AND VALIDATION OF A METHODOLOGICAL FRAMEWORK BASED ON MULTI-CRITERIA DECISION ANALYSIS (MCDA) FOR ORPHAN DRUGS
Antoni Gilabert-Perramon et al.
INTERNATIONAL JOURNAL OF TECHNOLOGY ASSESSMENT IN HEALTH CARE (2017)
Trial of Cannabidiol for Drug-Resistant Seizures in the Dravet Syndrome
Orrin Devinsky et al.
NEW ENGLAND JOURNAL OF MEDICINE (2017)
Optimizing the Diagnosis and Management of Dravet Syndrome: Recommendations From a North American Consensus Panel
Elaine C. Wirrell et al.
PEDIATRIC NEUROLOGY (2017)
DETERMINING THE VALUE OF SELEXIPAG FOR THE TREATMENT OF PULMONARY ARTERIAL HYPERTENSION (PAH) IN SPAIN BY MULTI-CRITERIA DECISION ANALYSIS (MCDA)
A. Jimenez et al.
VALUE IN HEALTH (2017)
Dravet syndrome: a new causative SCN1A mutation?
Martin Poryo et al.
CLINICAL CASE REPORTS (2017)
Appraising the holistic value of Lenvatinib for radio-iodine refractory differentiated thyroid cancer: A multi-country study applying pragmatic MCDA
Monika Wagner et al.
BMC CANCER (2017)
Mortality in Dravet syndrome: A review
Sharon Shmuely et al.
EPILEPSY & BEHAVIOR (2016)
Mortality in Dravet syndrome
Monica S. Cooper et al.
EPILEPSY RESEARCH (2016)
Multiple Criteria Decision Analysis for Health Care Decision Making-Emerging Good Practices: Report 2 of the ISPOR MCDA Emerging Good Practices Task Force
Kevin Marsh et al.
VALUE IN HEALTH (2016)
Multiple Criteria Decision Analysis for Health Care Decision Making-An Introduction: Report 1 of the ISPOR MCDA Emerging Good Practices Task Force
Praveen Thokala et al.
VALUE IN HEALTH (2016)
The PRISMA Extension Statement for Reporting of Systematic Reviews Incorporating Network Meta-analyses of Health Care Interventions: Checklist and Explanations
Brian Hutton et al.
ANNALS OF INTERNAL MEDICINE (2015)
Balancing costs and benefits at different stages of medical innovation: a systematic review of Multi-criteria decision analysis (MCDA)
Philip Wahlster et al.
BMC HEALTH SERVICES RESEARCH (2015)
The incidence of SCN1A-related Dravet syndrome in Denmark is 1: 22,000: A population-based study from 2004 to 2009
Allan Bayat et al.
EPILEPSIA (2015)
The European patient with Dravet syndrome: Results from a parent-reported survey on antiepileptic drug use in the European population with Dravet syndrome
Luis Miguel Aras et al.
EPILEPSY & BEHAVIOR (2015)
A Pilot Study of Multicriteria Decision Analysis for Valuing Orphan Medicines
Jon Sussex et al.
VALUE IN HEALTH (2013)
PHARE Trial results of subset analysis comparing 6 to 12 months of trastuzumab in adjuvant early breast cancer
X. Pivot et al.
CANCER RESEARCH (2012)
Bridging health technology assessment (HTA) with multicriteria decision analyses (MCDA): field testing of the EVIDEM framework for coverage decisions by a public payer in Canada
Michele Tony et al.
BMC HEALTH SERVICES RESEARCH (2011)
Current therapeutic procedures in Dravet syndrome
Catherine Chiron
DEVELOPMENTAL MEDICINE AND CHILD NEUROLOGY (2011)
Retrospective multiinstitutional study of the prevalence of early death in Dravet syndrome
Masako Sakauchi et al.
EPILEPSIA (2011)
Dravet syndrome: The long-term outcome
Pierre Genton et al.
EPILEPSIA (2011)
Child Neurology: Dravet syndrome When to suspect the diagnosis
John J. Millichap et al.
NEUROLOGY (2009)
Clobazam as add-on therapy in children with epileptic encephalopathy
RC Silva et al.
CANADIAN JOURNAL OF NEUROLOGICAL SCIENCES (2006)
Topiramate as add-on drug in severe myoclonic epilepsy in infancy: an Italian multicenter open trial
G Coppola et al.
EPILEPSY RESEARCH (2002)
分享论文
