相关参考文献
注意:仅列出部分参考文献,下载原文获取全部文献信息。Scratching the surface of RGD-directed AAV capsid engineering
Sergei Zolotukhin et al.
MOLECULAR THERAPY (2021)
High throughput screening of novel AAV capsids identifies variants for transduction of adult NSCs within the subventricular zone
Lukas P. M. Kremer et al.
MOLECULAR THERAPY-METHODS & CLINICAL DEVELOPMENT (2021)
Designer AAV muscle up
Carsten G. Bonnemann
CELL (2021)
Directed evolution of a family of AAV capsid variants enabling potent muscle-directed gene delivery across species
Mohammadsharif Tabebordbar et al.
CELL (2021)
Pre-arrayed Pan-AAV Peptide Display Libraries for Rapid Single-Round Screening
Kathleen Boerner et al.
MOLECULAR THERAPY (2020)
Engineering adeno-associated virus vectors for gene therapy
Chengwen Li et al.
NATURE REVIEWS GENETICS (2020)
U1 snRNP regulates cancer cell migration and invasion in vitro
Jung-Min Oh et al.
NATURE COMMUNICATIONS (2020)
Transcription Factor-Based Fate Specification and Forward Programming for Neural Regeneration
Lea J. Flitsch et al.
FRONTIERS IN CELLULAR NEUROSCIENCE (2020)
MV Capsid-Promoter Interactions Determine CNS Cell-Selective Gene Expression In Vivo
Sara K. Powell et al.
MOLECULAR THERAPY (2020)
Multiplexed Cre-dependent selection yields systemic AAVs for targeting distinct brain cell types
Sripriya Ravindra Kumar et al.
NATURE METHODS (2020)
The SLC25 Carrier Family: Important Transport Proteins in Mitochondrial Physiology and Pathology
Edmund R. S. Kunji et al.
PHYSIOLOGY (2020)
Identification of a myotropic AAV by massively parallel in vivo evaluation of barcoded capsid variants
Jonas Weinmann et al.
NATURE COMMUNICATIONS (2020)
Protocol for the Standardized Generation of Forward Programmed Cryopreservable Excitatory and Inhibitory Forebrain Neurons
Michael Peitz et al.
STAR PROTOCOLS (2020)
Adeno-associated virus vector as a platform for gene therapy delivery
Dan Wang et al.
NATURE REVIEWS DRUG DISCOVERY (2019)
Therapeutic AAV Gene Transfer to the Nervous System: A Clinical Reality
Eloise Hudry et al.
NEURON (2019)
Inducing Different Neuronal Subtypes from Astrocytes in the Injured Mouse Cerebral Cortex
Nicola Mattugini et al.
NEURON (2019)
Selective Targeting of Integrin αvβ8 by a Highly Active Cyclic Peptide
Florian Reichart et al.
JOURNAL OF MEDICINAL CHEMISTRY (2019)
Comparative AAV-eGFP Transgene Expression Using Vector Serotypes 1-9, 7m8, and 8b in Human Pluripotent Stem Cells, RPEs, and Human and Rat Cortical Neurons
Thu T. Duong et al.
STEM CELLS INTERNATIONAL (2019)
Synthetic AAV/CRISPR vectors for blocking HIV-1 expression in persistently infected astrocytes
Christine Kunze et al.
GLIA (2018)
AAVvector-mediated in vivo reprogramming into pluripotency
Elena Senis et al.
NATURE COMMUNICATIONS (2018)
New approaches for brain repair-from rescue to reprogramming
Roger A. Barkers et al.
NATURE (2018)
A stably self-renewing adult blood-derived induced neural stem cell exhibiting patternability and epigenetic rejuvenation
Chao Sheng et al.
NATURE COMMUNICATIONS (2018)
Optimization of design and production strategies for novel adeno-associated viral display peptide libraries
J. Koerbelin et al.
GENE THERAPY (2017)
Induction of functional dopamine neurons from human astrocytes in vitro and mouse astrocytes in a Parkinson's disease model
Pia Rivetti di Val Cervo et al.
NATURE BIOTECHNOLOGY (2017)
Cellular selectivity of AAV serotypes for gene delivery in neurons and astrocytes by neonatal intracerebroventricular injection
Sean L. Hammond et al.
PLOS ONE (2017)
Single-cut genome editing restores dystrophin expression in a new mouse model of muscular dystrophy
Leonela Amoasii et al.
SCIENCE TRANSLATIONAL MEDICINE (2017)
A Comprehensive Evaluation of the Activity and Selectivity Profile of Ligands for RGD-binding Integrins
Tobias G. Kapp et al.
SCIENTIFIC REPORTS (2017)
Development of novel AAV serotype 6 based vectors with selective tropism for human cancer cells
R. Sayroo et al.
GENE THERAPY (2016)
In Vivo Hepatic Reprogramming of Myofibroblasts with AAV Vectors as a Therapeutic Strategy for Liver Fibrosis
Milad Rezvani et al.
CELL STEM CELL (2016)
Evaluating cell reprogramming, differentiation and conversion technologies in neuroscience
Jerome Mertens et al.
NATURE REVIEWS NEUROSCIENCE (2016)
Mapping gene regulatory circuitry of Pax6 during neurogenesis
Sudhir Thakurela et al.
CELL DISCOVERY (2016)
Pluripotent Stem Cell-Derived Radial Glia-Like Cells as Stable Intermediate for Efficient Generation of Human Oligodendrocytes
Raphaela Gorris et al.
GLIA (2015)
Effectiveness of gene delivery systems for pluripotent and differentiated cells
Kleopatra Rapti et al.
MOLECULAR THERAPY-METHODS & CLINICAL DEVELOPMENT (2015)
Mitochondrial transporters of the SLC25 family and associated diseases: a review
Ferdinando Palmieri
JOURNAL OF INHERITED METABOLIC DISEASE (2014)
Engineering adeno-associated viruses for clinical gene therapy
Melissa A. Kotterman et al.
NATURE REVIEWS GENETICS (2014)
Rapid Single-Step Induction of Functional Neurons from Human Pluripotent Stem Cells
Yingsha Zhang et al.
NEURON (2013)
Derivation and Expansion Using Only Small Molecules of Human Neural Progenitors for Neurodegenerative Disease Modeling
Peter Reinhardt et al.
PLOS ONE (2013)
Environmental impact on direct neuronal reprogramming in vivo in the adult brain
Andrew Grande et al.
NATURE COMMUNICATIONS (2013)
Impact of capsid modifications by selected peptide ligands on recombinant adeno-associated virus serotype 2-mediated gene transduction
Matthias Naumer et al.
JOURNAL OF GENERAL VIROLOGY (2012)
Directed Evolution of Adeno-associated Virus for Enhanced Gene Delivery and Gene Targeting in Human Pluripotent Stem Cells
Prashanth Asuri et al.
MOLECULAR THERAPY (2012)
Improved structure, function and compatibility for CellProfiler: modular high-throughput image analysis software
Lee Kamentsky et al.
BIOINFORMATICS (2011)
An Evolved Adeno-associated Viral Variant Enhances Gene Delivery and Gene Targeting in Neural Stem Cells
Jae-Hyung Jang et al.
MOLECULAR THERAPY (2011)
From experimental setup to bioinformatics: An RNAi screening platform to identify host factors involved in HIV-1 replication
Kathleen Boerner et al.
BIOTECHNOLOGY JOURNAL (2010)
Modulation of Fate Determinants Olig2 and Pax6 in Resident Glia Evokes Spiking Neuroblasts in a Model of Mild Brain Ischemia
Golo Kronenberg et al.
STROKE (2010)
A rosette-type, self-renewing human ES cell-derived neural stem cell with potential for in vitro instruction and synaptic integration
Philipp Koch et al.
PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA (2009)
Directed evolution of adeno-associated virus to an infectious respiratory virus
Katherine J. D. A. Excoffon et al.
PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA (2009)
The Level of the Transcription Factor Pax6 Is Essential for Controlling the Balance between Neural Stem Cell Self-Renewal and Neurogenesis
Stephen N. Sansom et al.
PLOS GENETICS (2009)
In vitro and in vivo gene therapy vector evolution via multispecies interbreeding and retargeting of adeno-associated viruses
Dirk Grimm et al.
JOURNAL OF VIROLOGY (2008)
Pax6 promotes neurogenesis in human neural stem cells
Therese Kallur et al.
MOLECULAR AND CELLULAR NEUROSCIENCE (2008)
Expanded repertoire of AAV vector serotypes mediate unique patterns of transduction in mouse brain
Cassia N. Cearley et al.
MOLECULAR THERAPY (2008)
Concise review: Pax6 transcription factor contributes to both embryonic and adult neurogenesis as a multifunctional regulator
Noriko Osumi et al.
STEM CELLS (2008)
Induction of pluripotent stem cells from adult human fibroblasts by defined factors
Kazutoshi Takahashi et al.
CELL (2007)
Isolation of targeted AAV2 vectors from novel virus display libraries
Daniel A. Waterkamp et al.
JOURNAL OF GENE MEDICINE (2006)
Induction of pluripotent stem cells from mouse embryonic and adult fibroblast cultures by defined factors
Kazutoshi Takahashi et al.
CELL (2006)
Mosaic vectors comprised of modified AAV1 capsid proteins for efficient vector purification and targeting to vascular endothelial cells
M. D. Stachler et al.
GENE THERAPY (2006)
Regionalization and fate specification in neurospheres:: the role of Olig2 and Pax6
MA Hack et al.
MOLECULAR AND CELLULAR NEUROSCIENCE (2004)
Random peptide libraries displayed on adeno-associated virus to select for targeted gene therapy vectors
OJ Müller et al.
NATURE BIOTECHNOLOGY (2003)
In vitro selection of viral vectors with modified tropism:: The adeno-associated virus display
L Perabo et al.
MOLECULAR THERAPY (2003)
RGD inclusion in VP3 provides adeno-associated virus type 2 (AAV2)-based vectors with a heparan sulfate-independent cell entry mechanism
WF Shi et al.
MOLECULAR THERAPY (2003)
Glial cells generate neurons:: the role of the transcription factor Pax6
N Heins et al.
NATURE NEUROSCIENCE (2002)