期刊
FRONTIERS IN CELLULAR NEUROSCIENCE
卷 16, 期 -, 页码 -出版社
FRONTIERS MEDIA SA
DOI: 10.3389/fncel.2022.916065
关键词
spinal muscular atrophy (SMA); Survival Motor Neuron (SMN); onasemnogene abeparvovec; Zolgensma; AVXS-101; gene therapy; AAV9
资金
- NIH [R01 NS055925, US7838657]
- 2006 Presidential Early Career Award for Scientists and Engineers (PECASE) [R33 NS110960]
- DoD [W81XWH-19-1-0193]
- Iowa State University Library, Ames, Iowa