期刊
EXPERT OPINION ON THERAPEUTIC TARGETS
卷 26, 期 5, 页码 393-399出版社
TAYLOR & FRANCIS LTD
DOI: 10.1080/14728222.2022.2078699
关键词
Hutchinson-Gilford progeria syndrome; farnesyltransferase (FTase); isoprenylcysteine carboxyl methyltransferase (ICMT); antisense oligonucleotide (ASO); gene editing; CRISPR/Cas9; adenine base editor (ABE)
资金
- Spanish Ministerio de Ciencia e Innovacion (MCIN)/Agencia Estatal de Investigacion (AEI) [PID2019-108489RB-I00]
- European Regional Development Fund ('A way to build Europe')
- Fundacio la Marato TV3 [202033]
- Progeria Research Foundation (PRF) [PRF 2019-77]
- Asociacion Progeria Alexandra Peraut
- PRF
- Swedish Research Council
- Comunidad Autonoma de Madrid [2017-T1/BMD5247]
- Instituto de Salud Carlos III
- Pro-CNIC Foundation
- MCIN/AEI [CEX2020-001041-S]
- Center for Innovative Medicine