3.9 Review

Applications and challenges of CR SPR-Cas gene-editing to disease treatment n clinics

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Summary: With over 466 million people worldwide affected by hearing loss, genetic factors contributing to 50% of congenital hearing loss, CRISPR-Cas9 systems offer new gene therapy strategies for treating genetic hearing impairment. This technology shows promise in targeted gene editing for deafness-associated genes and has the potential to revolutionize the treatment of genetic hearing diseases.

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