Precision medicine for genetic childhood movement disorders

Increasingly effective targeted precision medicine is either already available or in development for a number of genetic childhood movement disorders. Patient-centred, personalized approaches include the repurposing of existing treatments for specific conditions and the development of novel therapies that target the underlying genetic defect or disease mechanism. In tandem with these scientific advances, close collaboration between clinicians, researchers, affected families, and stakeholders in the wider community will be key to successfully delivering such precision therapies to children with movement disorders.

Automated summary

Targeted precision medicine is becoming increasingly important in treating genetic childhood movement disorders, with personalized approaches including repurposing existing treatments and developing new therapies. Close collaboration between clinicians, researchers, affected families, and stakeholders in the wider community is crucial for successfully delivering these precision therapies to children with movement disorders.