期刊
CIRCULATION
卷 134, 期 11, 页码 777-779出版社
LIPPINCOTT WILLIAMS & WILKINS
DOI: 10.1161/CIRCULATIONAHA.116.024007
关键词
adeno-associated virus; CRISPR; gene therapy; genome; muscular dystrophy, duchenne
资金
- NHLBI NIH HHS [K08 HL094699] Funding Source: Medline