4.3 Article

Inotersen for the treatment of adults with polyneuropathy caused by hereditary transthyretin-mediated amyloidosis

相关参考文献

注意:仅列出部分参考文献,下载原文获取全部文献信息。
Article Clinical Neurology

Inotersen (transthyretin-specific antisense oligonucleotide) for treatment of transthyretin amyloidosis

Merrill D. Benson et al.

NEURODEGENERATIVE DISEASE MANAGEMENT (2019)

Article Clinical Neurology

Patisiran, an RNAi therapeutic for the treatment of hereditary transthyretin-mediated amyloidosis

Arnt Kristen et al.

NEURODEGENERATIVE DISEASE MANAGEMENT (2019)

Article Cardiac & Cardiovascular Systems

TTR (Transthyretin) Stabilizers Are Associated With Improved Survival in Patients With TTR Cardiac Amyloidosis

Hannah Rosenblum et al.

CIRCULATION-HEART FAILURE (2018)

Article Clinical Neurology

Estimating the global prevalence of transthyretin familial amyloid polyneuropathy

Hartmut H. Schmidt et al.

MUSCLE & NERVE (2018)

Article Medicine, General & Internal

Patisiran, an RNAi Therapeutic, for Hereditary Transthyretin Amyloidosis

D. Adams et al.

NEW ENGLAND JOURNAL OF MEDICINE (2018)

Article Medicine, General & Internal

Inotersen Treatment for Patients with Hereditary Transthyretin Amyloidosis

M. D. Benson et al.

NEW ENGLAND JOURNAL OF MEDICINE (2018)

Article Biochemistry & Molecular Biology

Hereditary transthyretin amyloidosis: baseline characteristics of patients in the NEURO-TTR trial

Marcia Waddington-Cruz et al.

AMYLOID-JOURNAL OF PROTEIN FOLDING DISORDERS (2018)

Article Medicine, General & Internal

Tafamidis Treatment for Patients with Transthyretin Amyloid Cardiomyopathy

Mathew S. Maurer et al.

NEW ENGLAND JOURNAL OF MEDICINE (2018)

Article Biochemistry & Molecular Biology

Long-term safety and efficacy of tafamidis for the treatment of hereditary transthyretin amyloid polyneuropathy: results up to 6 years

Fabio A. Barroso et al.

AMYLOID-JOURNAL OF PROTEIN FOLDING DISORDERS (2017)

Article Medicine, General & Internal

Cardiac amyloidosis : An update on diagnosis and treatment

Joseph P. Donnelly et al.

CLEVELAND CLINIC JOURNAL OF MEDICINE (2017)

Article Biochemistry & Molecular Biology

Safety and efficacy of a TTR specific antisense oligonucleotide in patients with transthyretin amyloid cardiomyopathy

Merrill D. Benson et al.

AMYLOID-JOURNAL OF PROTEIN FOLDING DISORDERS (2017)

Article Biochemistry & Molecular Biology

CSP-1103 (CHF5074) stabilizes human transthyretin in healthy human subjects

Lixia Qiang et al.

AMYLOID-JOURNAL OF PROTEIN FOLDING DISORDERS (2017)

Review Medicine, Research & Experimental

Transthyretin amyloidosis: an under-recognized neuropathy and cardiomyopathy

Natalie J. Galant et al.

CLINICAL SCIENCE (2017)

Article Biochemistry & Molecular Biology

Suppressing transthyretin production in mice, monkeys and humans using 2nd-Generation antisense oligonucleotides

Elizabeth J. Ackermann et al.

AMYLOID-JOURNAL OF PROTEIN FOLDING DISORDERS (2016)

Article Biochemistry & Molecular Biology

Novel conformation-specific monoclonal antibodies against amyloidogenic forms of transthyretin

Jeffrey N. Higaki et al.

AMYLOID-JOURNAL OF PROTEIN FOLDING DISORDERS (2016)

Review Clinical Neurology

Red-flag symptom clusters in transthyretin familial amyloid polyneuropathy

Isabel Conceicao et al.

JOURNAL OF THE PERIPHERAL NERVOUS SYSTEM (2016)

Review Clinical Neurology

Management of asymptomatic gene carriers of transthyretin familial amyloid polyneuropathy

Hartmut H-J. Schmidt et al.

MUSCLE & NERVE (2016)

Article Multidisciplinary Sciences

Repositioning tolcapone as a potent inhibitor of transthyretin amyloidogenesis and associated cellular toxicity

Ricardo Sant'Anna et al.

NATURE COMMUNICATIONS (2016)

Article Surgery

Outcomes After Heart Transplantation for Amyloid Cardiomyopathy in the Modern Era

M. K. Davis et al.

AMERICAN JOURNAL OF TRANSPLANTATION (2015)

Article Biochemistry & Molecular Biology

Ophthalmological manifestations in hereditary transthyretin (ATTR V30M) carriers: a review of 513 cases

Joao Melo Beirao et al.

AMYLOID-JOURNAL OF PROTEIN FOLDING DISORDERS (2015)

Review Medicine, General & Internal

Evolving landscape in the management of transthyretin amyloidosis

Philip N. Hawkins et al.

ANNALS OF MEDICINE (2015)

Article Medicine, General & Internal

Therapeutic Clearance of Amyloid by Antibodies to Serum Amyloid P Component

Duncan B. Richards et al.

NEW ENGLAND JOURNAL OF MEDICINE (2015)

Article Clinical Neurology

CNS involvement in V30M transthyretin amyloidosis: clinical, neuropathological and biochemical findings

Luis F. Maia et al.

JOURNAL OF NEUROLOGY NEUROSURGERY AND PSYCHIATRY (2015)

Article Genetics & Heredity

Online Registry for Mutations in Hereditary Amyloidosis Including Nomenclature Recommendations

Dorota M. Rowczenio et al.

HUMAN MUTATION (2014)

Article Medicine, General & Internal

Repurposing Diflunisal for Familial Amyloid Polyneuropathy A Randomized Clinical Trial

John L. Berk et al.

JAMA-JOURNAL OF THE AMERICAN MEDICAL ASSOCIATION (2013)

Review Genetics & Heredity

Guideline of transthyretin-related hereditary amyloidosis for clinicians

Yukio Ando et al.

ORPHANET JOURNAL OF RARE DISEASES (2013)

Article Multidisciplinary Sciences

AG10 inhibits amyloidogenesis and cellular toxicity of the familial amyloid cardiomyopathy-associated V122I transthyretin

Sravan C. Penchala et al.

PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA (2013)

Article Biochemistry & Molecular Biology

Doxycycline plus tauroursodeoxycholic acid for transthyretin amyloidosis: a phase II study

Laura Obici et al.

AMYLOID-JOURNAL OF PROTEIN FOLDING DISORDERS (2012)

Editorial Material Biotechnology & Applied Microbiology

Tafamidis

Gerard Said et al.

NATURE REVIEWS DRUG DISCOVERY (2012)

Article Cardiac & Cardiovascular Systems

Rate of Progression of Transthyretin Amyloidosis

Merrill D. Benson et al.

AMERICAN JOURNAL OF CARDIOLOGY (2011)

Article Medicine, Research & Experimental

Synergy of combined Doxycycline/TUDCA treatment in lowering Transthyretin deposition and associated biomarkers: studies in FAP mouse models

Isabel Cardoso et al.

JOURNAL OF TRANSLATIONAL MEDICINE (2010)

Article Multidisciplinary Sciences

Trapping of palindromic ligands within native transthyretin prevents amyloid formation

Simon E. Kolstoe et al.

PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA (2010)