3.9 Article

Comparative Efficacy and Safety of Multiple Routes of Direct CNS Administration of Adeno-Associated Virus Gene Transfer Vector Serotype rh.10 Expressing the Human Arylsulfatase A cDNA to Nonhuman Primates

相关参考文献

注意:仅列出部分参考文献,下载原文获取全部文献信息。
Review Cell & Tissue Engineering

Advances and Pitfalls of Cell Therapy in Metabolic Leukodystrophies

Catarina Oliveira Miranda et al.

CELL TRANSPLANTATION (2013)

Letter Biotechnology & Applied Microbiology

Mouse Gender Influences Brain Transduction by Intravascularly Administered AAV9

Casey A. Maguire et al.

MOLECULAR THERAPY (2013)

Review Neurosciences

Gene therapy and neurodevelopmental disorders

Steven James Gray

NEUROPHARMACOLOGY (2013)

Article Multidisciplinary Sciences

Lentiviral Hematopoietic Stem Cell Gene Therapy Benefits Metachromatic Leukodystrophy

Alessandra Biffi et al.

SCIENCE (2013)

Article Biotechnology & Applied Microbiology

Correction of Brain Oligodendrocytes by AAVrh.10 Intracerebral Gene Therapy in Metachromatic Leukodystrophy Mice

Francoise Piguet et al.

HUMAN GENE THERAPY (2012)

Article Biochemistry & Molecular Biology

Efficacy of enzyme replacement therapy in an aggravated mouse model of metachromatic leukodystrophy declines with age

Frank Matthes et al.

HUMAN MOLECULAR GENETICS (2012)

Review Biochemistry & Molecular Biology

Role of sulfatide in normal and pathological cells and tissues

Tadanobu Takahashi et al.

JOURNAL OF LIPID RESEARCH (2012)

Review Endocrinology & Metabolism

Developing treatment options for metachromatic leukodystrophy

Spyros P. Batzios et al.

MOLECULAR GENETICS AND METABOLISM (2012)

Article Biochemistry & Molecular Biology

Efficient intracerebral delivery of AAV5 vector encoding human ARSA in non-human primate

Marie-Anne Colle et al.

HUMAN MOLECULAR GENETICS (2010)

Article Veterinary Sciences

Clinical chemistry and hematology values in a Caribbean population of African green monkeys

Shervin Liddie et al.

JOURNAL OF MEDICAL PRIMATOLOGY (2010)

Article Clinical Neurology

Gene therapy for late infantile neuronal ceroid lipofuscinosis: neurosurgical considerations Clinical article

Mark M. Souweidane et al.

JOURNAL OF NEUROSURGERY-PEDIATRICS (2010)

Review Clinical Neurology

Metachromatic Leukodystrophy - An Update

V. Gieselmann et al.

NEUROPEDIATRICS (2010)

Review Biochemistry & Molecular Biology

Immunity to adeno-associated virus vectors in animals and humans: a continued challenge

A. K. Zaiss et al.

GENE THERAPY (2008)

Review Neurosciences

The origin and cell lineage of microglia - New concepts

W. Y. Chan et al.

BRAIN RESEARCH REVIEWS (2007)

Article Medicine, Research & Experimental

Gene therapy of metachromatic leukodystrophy reverses neurological damage and deficits mice

Alessandra Biffi et al.

JOURNAL OF CLINICAL INVESTIGATION (2006)

Article Biotechnology & Applied Microbiology

Immune responses to AAV in a phase I study for Canavan disease

S. W. J. McPhee et al.

JOURNAL OF GENE MEDICINE (2006)

Article Biochemistry & Molecular Biology

Enzyme replacement improves nervous system pathology and function in a mouse model for metachromatic leukodystrophy

U Matzner et al.

HUMAN MOLECULAR GENETICS (2005)

Article Multidisciplinary Sciences

Human CD34+ cells differentiate into microglia and express recombinant therapeutic protein

M Asheuer et al.

PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA (2004)

Review Cell Biology

Mannose 6-phosphate receptors: New twists in the tale

P Ghosh et al.

NATURE REVIEWS MOLECULAR CELL BIOLOGY (2003)