相关参考文献
注意:仅列出部分参考文献,下载原文获取全部文献信息。3′UTR-truncated Hmga2 cDNA causes MPN-like hematopoiesis by conferring a clonal growth advantage at the level of HSC in mice
Kazuhiko Ikeda et al.
BLOOD (2011)
A preclinical approach for gene therapy of beta-thalassemia
Laura Breda et al.
COOLEY'S ANEMIA: NINTH SYMPOSIUM (2010)
Strategy for a multicenter phase I clinical trial to evaluate globin gene transfer in beta-thalassemia
Michel Sadelain et al.
COOLEY'S ANEMIA: NINTH SYMPOSIUM (2010)
Mutation of a barrier insulator in the human ankyrin-1 gene is associated with hereditary spherocytosis
Patrick G. Gallagher et al.
JOURNAL OF CLINICAL INVESTIGATION (2010)
Transfusion independence and HMGA2 activation after gene therapy of human β-thalassaemia
Marina Cavazzana-Calvo et al.
NATURE (2010)
The 3′ Region of the Chicken Hypersensitive Site-4 Insulator Has Properties Similar to Its Core and Is Required for Full Insulator Activity
Paritha I. Arumugam et al.
PLOS ONE (2009)
Resolving the distinct stages in erythroid differentiation based on dynamic changes in membrane protein expression during erythropoiesis
Ke Chen et al.
PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA (2009)
On the road to gene therapy for beta-thalassemia and sickle cell anemia
Arthur Bank
PEDIATRIC HEMATOLOGY AND ONCOLOGY (2008)
In vivo selection of genetically modified erythroblastic progenitors leads to long-term correction of β-thalassemia
Annarita Miccio et al.
PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA (2008)
We gather together: insulators and genome organization
Julie A. Wallace et al.
CURRENT OPINION IN GENETICS & DEVELOPMENT (2007)
Therapeutic options for patients with severe beta-thalassemia: The need for globin gene therapy
Michel Sadelain et al.
HUMAN GENE THERAPY (2007)
Insulators: exploiting transcriptional and epigenetic mechanisms
Miklos Gaszner et al.
NATURE REVIEWS GENETICS (2006)
Different steroids co-regulate long-term expansion versus terminal differentiation in primary human erythroid progenitors
C Leberbauer et al.
BLOOD (2005)
Successful correction of the human β-thalassemia major phenotype using a lentiviral vector
G Puthenveetil et al.
BLOOD (2004)
Successful treatment of murine β-thalassemia using in vivo selection of genetically modified, drug-resistant hematopoietic stem cells
DA Persons et al.
BLOOD (2003)
A novel murine model of Cooley anemia and its rescue by lentiviral-mediated human β-globin gene transfer
S Rivella et al.
BLOOD (2003)
Permanent and panerythroid correction of murine β thalassemia by multiple lentiviral integration in hematopoietic stem cells
S Imren et al.
PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA (2002)
Successful treatment of murine β-thalassemia intermedia by transfer of the human β-globin gene
C May et al.
BLOOD (2002)
Correction of sickle cell disease in transgenic mouse models by gene therapy
R Pawliuk et al.
SCIENCE (2001)
Therapeutic haemoglobin synthesis in β-thalassaemic mice expressing lentivirus-encoded human β-globin
C May et al.
NATURE (2000)
The cHS4 insulator increases the probability of retroviral expression at random chromosomal integration sites
S Rivella et al.
JOURNAL OF VIROLOGY (2000)