4.6 Article

Marginal Level Dystrophin Expression Improves Clinical Outcome in a Strain of Dystrophin/Utrophin Double Knockout Mice

相关参考文献

注意:仅列出部分参考文献,下载原文获取全部文献信息。
Article Pathology

Genetic Background Affects Properties of Satellite Cells and mdx Phenotypes

So-ichiro Fukada et al.

AMERICAN JOURNAL OF PATHOLOGY (2010)

Article Biochemistry & Molecular Biology

Flt-1 haploinsufficiency ameliorates muscular dystrophy phenotype by developmentally increased vasculature in mdx mice

Mayank Verma et al.

HUMAN MOLECULAR GENETICS (2010)

Article Clinical Neurology

GENDER INFLUENCES CARDIAC FUNCTION IN THE mdx MODEL OF DUCHENNE CARDIOMYOPATHY

Brian Bostick et al.

MUSCLE & NERVE (2010)

Article Clinical Neurology

Coinheritance of Noonan syndrome and Becker muscular dystrophy

Argirios Dinopoulos et al.

NEUROMUSCULAR DISORDERS (2010)

Article Biochemistry & Molecular Biology

Personalised Genetic Intervention for Duchenne Muscular Dystrophy: Antisense Oligomers and Exon Skipping

Chalermchai Mitrpant et al.

Current Molecular Pharmacology (2010)

Article Biochemistry & Molecular Biology

Sub-physiological sarcoglycan expression contributes to compensatory muscle protection in mdx mice

Dejia Li et al.

HUMAN MOLECULAR GENETICS (2009)

Article Medicine, Research & Experimental

Latent TGF-β-binding protein 4 modifies muscular dystrophy in mice

Ahlke Heydemann et al.

JOURNAL OF CLINICAL INVESTIGATION (2009)

Article Clinical Neurology

Dystrophin levels as low as 30% are sufficient to avoid muscular dystrophy in the human

Marcella Neri et al.

NEUROMUSCULAR DISORDERS (2007)

Article Biochemistry & Molecular Biology

Dystrophin-deficient mdx mice display a reduced life span and are susceptible to spontaneous rhabdomyosarcoma

Jeffrey S. Chamberlain et al.

FASEB JOURNAL (2007)

Article Multidisciplinary Sciences

PTC124 targets genetic disorders caused by nonsense mutations

Ellen M. Welch et al.

NATURE (2007)

Article Biochemistry & Molecular Biology

rAAV6-microdystrophin preserves muscle function and extends lifespan in severely dystrophic mice

Paul Gregorevic et al.

NATURE MEDICINE (2006)

Article Biotechnology & Applied Microbiology

Efficient in vivo gene expression by trans-splicing adeno-associated viral vectors

Y Lai et al.

NATURE BIOTECHNOLOGY (2005)