4.8 Article

Site-specific integration and tailoring of cassette design for sustainable gene transfer

相关参考文献

注意:仅列出部分参考文献,下载原文获取全部文献信息。
Letter Infectious Diseases

Frequency of CCR5 genotypes in HIV-infected patients in Roraima, Brazil

Andre de Lima Guerra Corado et al.

BRAZILIAN JOURNAL OF INFECTIOUS DISEASES (2016)

Article Biotechnology & Applied Microbiology

Genomic safe harbors permit high beta-globin transgene expression in thalassemia induced pluripotent stem cells

Eirini P. Papapetrou et al.

NATURE BIOTECHNOLOGY (2011)

Review Genetics & Heredity

Charting histone modifications and the functional organization of mammalian genomes

Vicky W. Zhou et al.

NATURE REVIEWS GENETICS (2011)

Review Genetics & Heredity

Ex vivo gene transfer and correction for cell-based therapies

Luigi Naldini

NATURE REVIEWS GENETICS (2011)

Article Multidisciplinary Sciences

Transfusion independence and HMGA2 activation after gene therapy of human β-thalassaemia

Marina Cavazzana-Calvo et al.

NATURE (2010)

Review Genetics & Heredity

Genome editing with engineered zinc finger nucleases

Fyodor D. Urnov et al.

NATURE REVIEWS GENETICS (2010)

Review Biochemistry & Molecular Biology

Next-generation gene targeting in the mouse for functional genomics

Yoichi Gondo et al.

BMB REPORTS (2009)

Article Biochemistry & Molecular Biology

A small regulatory element from chromosome 19 enhances liver-specific gene expression

C. Li et al.

GENE THERAPY (2009)

Article Biotechnology & Applied Microbiology

Efficient targeting of expressed and silent genes in human ESCs and iPSCs using zinc-finger nucleases

Dirk Hockemeyer et al.

NATURE BIOTECHNOLOGY (2009)

Review Genetics & Heredity

Human genetic variation and its contribution to complex traits

Kelly A. Frazer et al.

NATURE REVIEWS GENETICS (2009)

Article Medicine, General & Internal

Gene Therapy for Immunodeficiency Due to Adenosine Deaminase Deficiency.

Alessandro Aiuti et al.

NEW ENGLAND JOURNAL OF MEDICINE (2009)

Article Biochemistry & Molecular Biology

More than a decade of developmental gene expression atlases: where are we now?

Bouke A. de Boer et al.

NUCLEIC ACIDS RESEARCH (2009)

Article Multidisciplinary Sciences

Site-specific integration of adeno-associated virus involves partial duplication of the target locus

Els Henckaerts et al.

PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA (2009)

Review Biochemistry & Molecular Biology

Progress and prospects: Zinc-finger nucleases as gene therapy agents

D. Carroll

GENE THERAPY (2008)

Article Biochemistry & Molecular Biology

Rapid Open-Source engineering of customized zinc-finger nucleases for highly efficient gene modification

Morgan L. Maeder et al.

MOLECULAR CELL (2008)

Article Biochemistry & Molecular Biology

Induction of pluripotent stem cells from adult human fibroblasts by defined factors

Kazutoshi Takahashi et al.

Article Biotechnology & Applied Microbiology

Gene editing in human stem cells using zinc finger nucleases and integrase-defective lentiviral vector delivery

Angelo Lombardo et al.

NATURE BIOTECHNOLOGY (2007)

Article Biotechnology & Applied Microbiology

An improved zinc-finger nuclease architecture for highly specific genome editing

Jeffrey C. Miller et al.

NATURE BIOTECHNOLOGY (2007)

Article Biotechnology & Applied Microbiology

A ROCK inhibitor permits survival of dissociated human embryonic stem cells

Kiichi Watanabe et al.

NATURE BIOTECHNOLOGY (2007)

Article Biochemical Research Methods

Chromatin immunoprecipitation and microarray-based analysis of protein location

Tong Ihn Lee et al.

NATURE PROTOCOLS (2006)

Review Biotechnology & Applied Microbiology

Silencing and variegation of gammaretrovirus and lentivirus vectors

J Ellis

HUMAN GENE THERAPY (2005)

Article Biochemical Research Methods

Comprehensive algorithm for quantitative real-time polymerase chain reaction

S Zhao et al.

JOURNAL OF COMPUTATIONAL BIOLOGY (2005)

Article Multidisciplinary Sciences

Chimeric nucleases stimulate gene targeting in human cells

MH Porteus et al.

SCIENCE (2003)

Article Biochemistry & Molecular Biology

A new mathematical model for relative quantification in real-time RT-PCR

MW Pfaffl

NUCLEIC ACIDS RESEARCH (2001)