4.8 Article

Linking SNPs to CAG repeat length in Huntington's disease patients

相关参考文献

注意:仅列出部分参考文献,下载原文获取全部文献信息。
Article Genetics & Heredity

Fear of health insurance loss among individuals at risk for Huntington disease

Emily Oster et al.

AMERICAN JOURNAL OF MEDICAL GENETICS PART A (2008)

Article Biotechnology & Applied Microbiology

Identification and allele-specific silencing of the mutant huntingtin allele in Huntington's disease patient-derived fibroblasts

P. H. J. van Bilsen et al.

HUMAN GENE THERAPY (2008)

Article Multidisciplinary Sciences

Therapeutic silencing of mutant huntingtin with siRNA attenuates striatal and cortical neuropathology and behavioral deficits

M. DiFiglia et al.

PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA (2007)

Article Genetics & Heredity

Designing siRNA that distinguish between genes that differ by a single nucleotide

Dianne S. Schwarz et al.

PLOS GENETICS (2006)

Article Multidisciplinary Sciences

Allele-specific silencing of dominant disease genes

VM Miller et al.

PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA (2003)

Article Biochemistry & Molecular Biology

Rescue of polyglutamine-mediated cytotoxicity by double-stranded RNA-mediated RNA interference

NJ Caplen et al.

HUMAN MOLECULAR GENETICS (2002)