4.5 Article

Incentives for Starting Small Companies Focused on Rare and Neglected Diseases

相关参考文献

注意:仅列出部分参考文献,下载原文获取全部文献信息。
Review Pharmacology & Pharmacy

An analysis of original research contributions toward FDA-approved drugs

Eric V. Patridge et al.

DRUG DISCOVERY TODAY (2015)

Editorial Material Medicine, General & Internal

Experience With the Priority Review Voucher Program for Drug Development

Aaron S. Kesselheim et al.

JAMA-JOURNAL OF THE AMERICAN MEDICAL ASSOCIATION (2015)

News Item Biotechnology & Applied Microbiology

21st Century Cures Act wins in US House

[Anonymous]

NATURE BIOTECHNOLOGY (2015)

Editorial Material Chemistry, Medicinal

Incentives to Repurpose Existing Drugs for Orphan Indications

Annette K. Kwok et al.

ACS MEDICINAL CHEMISTRY LETTERS (2015)

Review Chemistry, Medicinal

The use of the United States FDA programs as a strategy to advance the development of drug products for neglected tropical diseases

Kristina Sachs-Barrable et al.

DRUG DEVELOPMENT AND INDUSTRIAL PHARMACY (2014)

Article Chemistry, Medicinal

The discovery of medicines for rare diseases

David C. Swinney et al.

FUTURE MEDICINAL CHEMISTRY (2014)

Review Pharmacology & Pharmacy

Multifaceted roles of ultra-rare and rare disease patients/parents in drug discovery

Jill Wood et al.

DRUG DISCOVERY TODAY (2013)

Review Genetics & Heredity

A generalizable pre-clinical research approach for orphan disease therapy

Chandree L. Beaulieu et al.

ORPHANET JOURNAL OF RARE DISEASES (2012)

Article Endocrinology & Metabolism

Sanfilippo syndrome: A mini-review

M. J. Valstar et al.

JOURNAL OF INHERITED METABOLIC DISEASE (2008)