4.0 Article

Safety Pharmacology and Genotoxicity Evaluation of AVI-4658

相关参考文献

注意:仅列出部分参考文献,下载原文获取全部文献信息。
Article Clinical Neurology

Efficacy of Systemic Morpholino Exon-Skipping in Duchenne Dystrophy Dogs

Toshifumi Yokota et al.

ANNALS OF NEUROLOGY (2009)

Meeting Abstract Clinical Neurology

A phase I/IIa study on antisense compound PRO051 in patients with Duchenne muscular dystrophy

N. M. Goemans et al.

NEUROMUSCULAR DISORDERS (2009)

Review Biochemistry & Molecular Biology

Therapeutic Potential of Splice-Switching Oligonucleotides

John Bauman et al.

OLIGONUCLEOTIDES (2009)

Review Pharmacology & Pharmacy

Antisense, RNAi, and gene silencing strategies for therapy: Mission possible or impossible?

Elizabeth R. Rayburn et al.

DRUG DISCOVERY TODAY (2008)

Article Medicine, General & Internal

Local dystrophin restoration with antisense oligonucleotide PRO051

Judith C. van Deutekom et al.

NEW ENGLAND JOURNAL OF MEDICINE (2007)

Article Biochemistry & Molecular Biology

Antisense oligonucleotides containing locked nucleic acid improve potency but cause significant hepatotoxicity in animals

Eric E. Swayze et al.

NUCLEIC ACIDS RESEARCH (2007)

Article Biochemistry & Molecular Biology

Therapeutic antisense-induced exon skipping in cultured muscle cells from six different DMD patients

A Aartsma-Rus et al.

HUMAN MOLECULAR GENETICS (2003)

Article Clinical Neurology

Early prednisone treatment in Duchenne muscular dystrophy

L Merlini et al.

MUSCLE & NERVE (2003)

Review Medicine, General & Internal

The muscular dystrophies

AEH Emery

LANCET (2002)

Article Biochemistry & Molecular Biology

Antisense-induced exon skipping restores dystrophin expression in DMD patient derived muscle cells

JCT van Deutekom et al.

HUMAN MOLECULAR GENETICS (2001)

Article Cell Biology

Cross-talk between pro-inflammatory transcription factors and glucocorticoids

IM Adcock et al.

IMMUNOLOGY AND CELL BIOLOGY (2001)