相关参考文献
注意：仅列出部分参考文献，下载原文获取全部文献信息。Axonal transport of adeno-associated viral vectors is serotype-dependent
E. A. Salegio et al.
GENE THERAPY (2013)
Strong Cortical and Spinal Cord Transduction After AAV7 and AAV9 Delivery into the Cerebrospinal Fluid of Nonhuman Primates
Lluis Samaranch et al.
HUMAN GENE THERAPY (2013)
Corticospinal tract transduction: a comparison of seven adeno-associated viral vector serotypes and a non-integrating lentiviral vector
T. H. Hutson et al.
GENE THERAPY (2012)
Robust spinal motor neuron transduction following intrathecal delivery of AAV9 in pigs
T. Federici et al.
GENE THERAPY (2012)
Decreasing Disease Severity in Symptomatic, Smn-/-; SMN2+/+, Spinal Muscular Atrophy Mice Following scAAV9-SMN Delivery
Jacqueline J. Glascock et al.
HUMAN GENE THERAPY (2012)
Adeno-Associated Virus Serotype 9 Transduction in the Central Nervous System of Nonhuman Primates
Lluis Samaranch et al.
HUMAN GENE THERAPY (2012)
Failure of lower motor neuron radial outgrowth precedes retrograde degeneration in a feline model of spinal muscular atrophy
Erin N. Wakeling et al.
JOURNAL OF COMPARATIVE NEUROLOGY (2012)
IGF-1 delivery to CNS attenuates motor neuron cell death but does not improve motor function in type III SMA mice
Li-Kai Tsai et al.
NEUROBIOLOGY OF DISEASE (2012)
Comparison of Adeno-Associated Viral Vector Serotypes for Spinal Cord and Motor Neuron Gene Delivery
Brooke R. Snyder et al.
HUMAN GENE THERAPY (2011)
Optimizing Promoters for Recombinant Adeno-Associated Virus-Mediated Gene Expression in the Peripheral and Central Nervous System Using Self-Complementary Vectors
Steven J. Gray et al.
HUMAN GENE THERAPY (2011)
Intravenous scAAV9 delivery of a codon-optimized SMN1 sequence rescues SMA mice
Elisa Dominguez et al.
HUMAN MOLECULAR GENETICS (2011)
Preclinical Differences of Intravascular AAV9 Delivery to Neurons and Glia: A Comparative Study of Adult Mice and Nonhuman Primates
Steven J. Gray et al.
MOLECULAR THERAPY (2011)
Systemic Gene Delivery in Large Species for Targeting Spinal Cord, Brain, and Peripheral Tissues for Pediatric Disorders
Adam K. Bevan et al.
MOLECULAR THERAPY (2011)
Peripheral SMN restoration is essential for long-term rescue of a severe spinal muscular atrophy mouse model
Yimin Hua et al.
NATURE (2011)
Conjoint pathologic cascades mediated by ALS/FTLD-U linked RNA-binding proteins TDP-43 and FUS
Daisuke Ito et al.
NEUROLOGY (2011)
Efficient transduction of non-human primate motor neurons after intramuscular delivery of recombinant AAV serotype 6
C. Towne et al.
GENE THERAPY (2010)
Cardiac defects contribute to the pathology of spinal muscular atrophy models
Monir Shababi et al.
HUMAN MOLECULAR GENETICS (2010)
Restoration of central nervous system α-N-acetylglucosaminidase activity and therapeutic benefits in mucopolysaccharidosis IIIB mice by a single intracisternal recombinant adeno-associated viral type 2 vector delivery
Haiyan Fu et al.
JOURNAL OF GENE MEDICINE (2010)
Rescue of the spinal muscular atrophy phenotype in a mouse model by early postnatal delivery of SMN
Kevin D. Foust et al.
NATURE BIOTECHNOLOGY (2010)
RNA processing pathways in amyotrophic lateral sclerosis
Marka van Blitterswijk et al.
NEUROGENETICS (2010)
Erythropoietin in amyotrophic lateral sclerosis: A pilot, randomized, double-blind, placebo-controlled study of safety and tolerability
Giuseppe Lauria et al.
AMYOTROPHIC LATERAL SCLEROSIS (2009)
Global diffuse distribution in the brain and efficient gene delivery to the dorsal root ganglia by intrathecal injection of adeno-associated viral vector serotype 1
Naotaka Iwamoto et al.
JOURNAL OF GENE MEDICINE (2009)
Intravenous Administration of Self-complementary AAV9 Enables Transgene Delivery to Adult Motor Neurons
Sandra Duque et al.
MOLECULAR THERAPY (2009)
Intravascular AAV9 preferentially targets neonatal neurons and adult astrocytes
Kevin D. Foust et al.
NATURE BIOTECHNOLOGY (2009)
Recombinant adeno-asociated virus-mediated global anterograde delivery of glial cell line-derived neurotrophic factor to the spinal cord: Comparison of rubrospinal and corticospinal tracts in the rat
Kevin D. Foust et al.
HUMAN GENE THERAPY (2008)
Reduced SMN protein impairs maturation of the neuromuscular junctions in mouse models of spinal muscular atrophy
Shingo Kariya et al.
HUMAN MOLECULAR GENETICS (2008)
Delivery of AAV-IGF-1 to the CNS extends survival in ALS mice through modification of aberrant glial cell activity
James C. Dodge et al.
MOLECULAR THERAPY (2008)
Efficient retrograde neuronal transduction utilizing self-complementary AAV1
Edmund R. Hollis et al.
MOLECULAR THERAPY (2008)
Sensory neuron targeting by self-complementary AAV8 via lumbar puncture for chronic pain
Benjamin Storek et al.
PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA (2008)
An ∼140-kb deletion associated with feline spinal muscular atrophy implies an essential LIX1 function for motor neuron survival
John C. Fyfe et al.
GENOME RESEARCH (2006)
Gene therapy of the brain in the dog model of Hurler's syndrome
Carine Ciron et al.
ANNALS OF NEUROLOGY (2006)
Anthrax lethal toxin induces ketotifen-sensitive intradermal vascular leakage in certain inbred mice
Y Gozes et al.
INFECTION AND IMMUNITY (2006)
Expression of vascular endothelial growth factor and its receptors in the central nervous system in amyotrophic lateral sclerosis
A Brockington et al.
JOURNAL OF NEUROPATHOLOGY AND EXPERIMENTAL NEUROLOGY (2006)
From angiogenesis to neuropathology
DA Greenberg et al.
NATURE (2005)
Inherited motor neuron disease in domestic cats: A model of spinal muscular atrophy
QC He et al.
PEDIATRIC RESEARCH (2005)
VEGF overexpression induces post-ischaemic neuroprotection, but facilitates haemodynamic steal phenomena
YM Wang et al.
BRAIN (2005)
Treatment of motoneuron degeneration by intracerebroventricular delivery of VEGF in a rat model of ALS
E Storkebaum et al.
NATURE NEUROSCIENCE (2005)
Low levels of the vascular endothelial growth factor in CSF from early ALS patients
D Devos et al.
NEUROLOGY (2004)
Deletion of murine Smn Exon 7 directed to liver leads to severe defect of liver development associated with iron overload
JM Vitte et al.
AMERICAN JOURNAL OF PATHOLOGY (2004)
β3-integrin regulates vascular endothelial growth factor-A-dependent permeability
SD Robinson et al.
ARTERIOSCLEROSIS THROMBOSIS AND VASCULAR BIOLOGY (2004)
VEGF delivery with retrogradely transported lentivector prolongs survival in a mouse ALS model
M Azzouz et al.
NATURE (2004)
A protein interaction map of Drosophila melanogaster
L Giot et al.
SCIENCE (2003)
Smn, the spinal muscular atrophy-determining gene product, modulates axon growth and localization of β-actin mRNA in growth cones of motoneurons
W Rossoll et al.
JOURNAL OF CELL BIOLOGY (2003)
Adeno-associated virus vector-mediated transduction in the cat brain
CH Vite et al.
GENE THERAPY (2003)
Knockdown of the survival motor neuron (Smn) protein in zebrafish causes defects in motor axon outgrowth and pathfinding
ML McWhorter et al.
JOURNAL OF CELL BIOLOGY (2003)
Retrograde viral delivery of IGF-1 prolongs survival in a mouse ALS model
BK Kaspar et al.
SCIENCE (2003)
VEGF is a modifier of amyotrophic lateral sclerosis in mice and humans and protects motoneurons against ischemic death
D Lambrechts et al.
NATURE GENETICS (2003)
The biology of VEGF and its receptors
N Ferrara et al.
NATURE MEDICINE (2003)
Cross-packaging of a single adeno-associated virus (AAV) type 2 vector genome into multiple AAV serotypes enables transduction with broad specificity
JE Rabinowitz et al.
JOURNAL OF VIROLOGY (2002)
Deletion of the hypoxia-response element in the vascular endothelial growth factor promoter causes motor neuron degeneration
B Oosthuyse et al.
NATURE GENETICS (2001)
A phase I/II trial of recombinant methionyl human brain derived neurotrophic factor administered by intrathecal infusion to patients with amyotrophic lateral sclerosis
G Ochs et al.
AMYOTROPHIC LATERAL SCLEROSIS AND OTHER MOTOR NEURON DISORDERS (2000)
The role of SMN in spinal muscular atrophy
S Jablonka et al.
JOURNAL OF NEUROLOGY (2000)
分享论文
