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Gemma L. Walmsley et al.
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Toshifumi Yokota et al.
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Chunping Qiao et al.
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Zejing Wang et al.
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Hermien E. Kan et al.
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Kathryn R. Wagner et al.
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Michela Alessandra Denti et al.
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Chunping Qiao et al.
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Myostatin directly regulates skeletal muscle fibrosis
Zhao Bo Li et al.
JOURNAL OF BIOLOGICAL CHEMISTRY (2008)
Myostatin blockade improves function but not histopathology in a murine model of limb-girdle muscular dystrophy 2C
Sasha Bogdanovich et al.
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Long-term skeletal muscle protection after gene transfer in a mouse model of LGMD-2D
Christina A. Pacak et al.
MOLECULAR THERAPY (2007)
Modulation of tolerance to the transgene product in a nonhuman primate model of AAV-mediated gene transfer to liver
Federico Mingozzi et al.
BLOOD (2007)
Sprinting without myrostatin: a genetic determinant of athletic prowess
Se-Jin Lee
TRENDS IN GENETICS (2007)
Quadrupling Muscle Mass in Mice by Targeting TGF-β Signaling Pathways
Se-Jin Lee
PLOS ONE (2007)
AAV-mediated delivery of a mutated myostatin propeptide ameliorates calpain 3 but not α-sarcoglycan deficiency
M. Bartoli et al.
GENE THERAPY (2007)
Sustained AAV-mediated dystrophin expression in a canine model of Duchenne muscular dystrophy with a brief course of immunosuppression
Zejing Wang et al.
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Myostatin does not regulate cardiac hypertrophy or fibrosis
Ronald D. Cohn et al.
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Contractile properties of EDL and soleus muscles of myostatin-deficient mice
Christopher L. Mendias et al.
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Entries in the Leiden Duchenne muscular dystrophy mutation database: An overview of mutation types and paradoxical cases that confirm the reading-frame rule
Annemieke Aartsma-Rus et al.
MUSCLE & NERVE (2006)
Body-wide gene therapy of Duchenne muscular dystrophy in the mdx mouse model
MA Denti et al.
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Characterization of alterations in diabetic myocardial tissue using high resolution MRI
R Loganathan et al.
INTERNATIONAL JOURNAL OF CARDIOVASCULAR IMAGING (2006)
Regulation of muscle growth by multiple ligands signaling through activin type II receptors
SJ Lee et al.
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Myostatin propeptide-mediated amelioration of dystrophic pathophysiology
S Bogdanovich et al.
FASEB JOURNAL (2005)
Adeno-associated virus-mediated microdystrophin expression protects young mdx muscle from contraction-induced injury
MJ Liu et al.
MOLECULAR THERAPY (2005)
Systemic delivery of genes to striated muscles using adeno-associated viral vectors
P Gregorevic et al.
NATURE MEDICINE (2004)
Rescue of dystrophic muscle through U7 snRNA-mediated exon skipping
A Goyenvalle et al.
SCIENCE (2004)
Brief report -: Myostatin mutation associated with gross muscle hypertrophy in a child
M Schuelke et al.
NEW ENGLAND JOURNAL OF MEDICINE (2004)
Regulation of muscle mass by myostatin
SJ Lee
ANNUAL REVIEW OF CELL AND DEVELOPMENTAL BIOLOGY (2004)
Activation of latent myostatin by the BMP-1/tolloid family of metalloproteinases
NM Wolfman et al.
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Origins and early descriptions of Duchenne muscular dystrophy
KL Tyler
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Canine X-linked muscular dystrophy in Japan (CXMDj)
Y Shimatsu et al.
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Dystrophin and mutations: one gene, several proteins, multiple phenotypes
F Muntoni et al.
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Loss of myostatin attenuates severity of muscular dystrophy in mdx mice
KR Wagner et al.
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Functional improvement of dystrophic muscle by myostatin blockade
S Bogdanovich et al.
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ER Barton et al.
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Modular flexibility of dystrophin: Implications for gene therapy of Duchenne muscular dystrophy
SQ Harper et al.
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Self-complementary recombinant adeno-associated virus (scAAV) vectors promote efficient transduction independently of DNA synthesis
DM McCarty et al.
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