4.5 Article

Validation of a mutated PRE sequence allowing high and sustained transgene expression while abrogating WHV-X protein synthesis: application to the gene therapy of WAS

Related references

Note: Only part of the references are listed.
Article Biotechnology & Applied Microbiology

Physiological promoters reduce the genotoxic risk of integrating gene vectors

Daniela Zychlinski et al.

MOLECULAR THERAPY (2008)

Article Gastroenterology & Hepatology

Lymphocyte-dependent and Th2 cytokine-associated colitis in mice deficient in Wiskott-Aldrich syndrome protein

Deanna D. Nguyen et al.

GASTROENTEROLOGY (2007)

Article Immunology

The Wiskott-Aldrich syndrome protein is required for the function of CD4+CD25+Foxp3+ regulatory T cells

Michel H. Maillard et al.

JOURNAL OF EXPERIMENTAL MEDICINE (2007)

Article Biotechnology & Applied Microbiology

Hematopoietic stem cell gene transfer in a tumor-prone mouse model uncovers low genotoxicity of lentiviral vector integration

Eugenio Montini et al.

NATURE BIOTECHNOLOGY (2006)

Article Biotechnology & Applied Microbiology

Oncogenesis following delivery of a nonprimate lentiviral gene therapy vector to fetal and neonatal mice

M Themis et al.

MOLECULAR THERAPY (2005)

Letter Biochemistry & Molecular Biology

Potential oncogene activity of the woodchuck hepatitis post-transcriptional regulatory element (WPRE)

SM Kingsman et al.

GENE THERAPY (2005)

Article Biochemistry & Molecular Biology

CRM1-dependent function of a cis-acting RNA export element

I Popa et al.

MOLECULAR AND CELLULAR BIOLOGY (2002)