Journal
EXPERT OPINION ON DRUG DISCOVERY
Volume 13, Issue 10, Pages 899-902Publisher
TAYLOR & FRANCIS LTD
DOI: 10.1080/17460441.2018.1514387
Keywords
Spinal muscular atrophy; motor neuron disease; gene therapy; survival motor neuron; therapy development
Categories
Funding
- Wellcome Trust [106098/Z/14/Z]