4.4 Article

Cyclodextrin-Based Iminosugar Click Clusters: The First Examples of Multivalent Pharmacological Chaperones for the Treatment of Lysosomal Storage Disorders

Journal

CHEMBIOCHEM
Volume 13, Issue 5, Pages 661-664

Publisher

WILEY-V C H VERLAG GMBH
DOI: 10.1002/cbic.201200005

Keywords

chaperones; cyclodextrins; Gaucher's disease; iminosugars; multivalency

Funding

  1. Institut Universitaire de France (IUF)
  2. CNRS [UMR 7509]
  3. University of Strasbourg
  4. Agence National de la Recherche (ANR) [08JC-0094-01]
  5. French Department of Research

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