Related references
Note: Only part of the references are listed.Gene Therapy for Immunodeficiency Due to Adenosine Deaminase Deficiency.
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Neonatal bone marrow transplantation of ADA-deficient SCID mice results in immunologic reconstitution despite low levels of engraftment and an absence of selective donor T lymphoid expansion
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Reduced thymic output, increased spontaneous apoptosis and oligoclonal B cells in polyethylene glycol-adenosine deaminase-treated patients
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Long-term efficacy of enzyme replacement therapy for Adenosine deaminase (ADA)-deficient Severe Combined Immunodeficiency (SCID)
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Clonal evidence for the transduction of CD34+ cells with lymphomyeloid differentiation potential and self-renewal capacity in the SCID-X1 gene therapy trial
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Persistence and expression of the adenosine deaminase gene for 12 years and immune reaction to gene transfer components: long-term results of the first clinical gene therapy trial
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Correction of ADA-SCID by stem cell gene therapy combined with nonmyeloablative conditioning
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Cognitive and behavioral abnormalities in adenosine deaminase deficient severe combined immunodeficiency
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Adenosine deaminase deficiency increases thymic apoptosis and causes defective T cell receptor signaling
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