4.7 Article

A novel human gamma-globin gene vector for genetic correction of sickle cell anemia in a humanized sickle mouse model: critical determinants for successful correction

Related references

Note: Only part of the references are listed.
Article Medicine, General & Internal

Gene Therapy for Immunodeficiency Due to Adenosine Deaminase Deficiency.

Alessandro Aiuti et al.

NEW ENGLAND JOURNAL OF MEDICINE (2009)

Article Hematology

Stable Long-Term Donor Engraftment following Reduced-Intensity Hematopoietic Cell Transplantation for Sickle Cell Disease

Lakshmanan Krishnamurti et al.

BIOLOGY OF BLOOD AND MARROW TRANSPLANTATION (2008)

Article Hematology

Circumstances of death in adult sickle cell disease patients

Deepika S. Darbari et al.

AMERICAN JOURNAL OF HEMATOLOGY (2006)

Article Biotechnology & Applied Microbiology

Hematopoietic stem cell gene transfer in a tumor-prone mouse model uncovers low genotoxicity of lentiviral vector integration

Eugenio Montini et al.

NATURE BIOTECHNOLOGY (2006)

Article Biotechnology & Applied Microbiology

A genetic strategy to treat sickle cell anemia by coregulating globin transgene expression and RNA interference

S Samakoglu et al.

NATURE BIOTECHNOLOGY (2006)

Article Medicine, General & Internal

Effect of hydroxyurea on mortality. and morbidity in adult sickle cell anemia - Risks and benefits up to 9 years of treatment

MH Steinberg et al.

JAMA-JOURNAL OF THE AMERICAN MEDICAL ASSOCIATION (2003)

Article Multidisciplinary Sciences

Correction of sickle cell disease in transgenic mouse models by gene therapy

R Pawliuk et al.

SCIENCE (2001)

Letter Medicine, General & Internal

Bone marrow transplantation without myeloablation for sickle cell disease.

L Krishnamurti et al.

NEW ENGLAND JOURNAL OF MEDICINE (2001)

Article Hematology

Stable mixed hematopoietic chimerism after bone marrow transplantation for sickle cell anemia

MC Walters et al.

BIOLOGY OF BLOOD AND MARROW TRANSPLANTATION (2001)

Article Biochemistry & Molecular Biology

Genetic correction of sickle cell disease: Insights using transgenic mouse models

MJ Blouin et al.

NATURE MEDICINE (2000)