4.7 Article

Antisense Oligonucleotide-based Splice Correction for USH2A-associated Retinal Degeneration Caused by a Frequent Deep-intronic Mutation

Journal

Molecular Therapy-Nucleic Acids
Volume 5, Issue -, Pages e381

Publisher

Elsevier BV
DOI: 10.1038/mtna.2016.89

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