4.6 Meeting Abstract

ALLELE-SELECTIVE INHIBITION OF MUTANT HTT TRANSCRIPTION THROUGHOUT THE BRAIN AFTER SUBCUTANEOUS ADMINISTRATION OF A PATROL™-ENABLED INVESTIGATIONAL GENETIC THERAPY IN THE R6/2 HUNTINGTON'S DISEASE TRANSGENIC MOUSE MODEL

Journal

JOURNAL OF NEUROLOGY NEUROSURGERY AND PSYCHIATRY
Volume 93, Issue -, Pages A86-A87

Publisher

BMJ PUBLISHING GROUP
DOI: 10.1136/jnnp-2022-ehdn.232

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