4.6 Article

Histopathological Defects in Intestine in Severe Spinal Muscular Atrophy Mice Are Improved by Systemic Antisense Oligonucleotide Treatment

Related references

Note: Only part of the references are listed.
Article Clinical Neurology

Vascular Defects and Spinal Cord Hypoxia in Spinal Muscular Atrophy

Eilidh Somers et al.

ANNALS OF NEUROLOGY (2016)

Correction Biochemistry & Molecular Biology

SMN deficiency disrupts gastrointestinal and enteric nervous system function in mice (vol 24, pg 3847, 2015)

Sara E. Gombash et al.

HUMAN MOLECULAR GENETICS (2015)

Article Biochemistry & Molecular Biology

SMN2 splice modulators enhance U1-pre-mRNA association and rescue SMA mice

James Palacino et al.

NATURE CHEMICAL BIOLOGY (2015)

Article Cell Biology

Vascular and neural stem cells in the gut: do they need each other?

Sandra Schrenk et al.

HISTOCHEMISTRY AND CELL BIOLOGY (2015)

Article Cell Biology

The monocyte-macrophage axis in the intestine

Calum C. Bain et al.

CELLULAR IMMUNOLOGY (2014)

Review Anatomy & Morphology

Spinal muscular atrophy: a motor neuron disorder or a multi-organ disease?

Monir Shababi et al.

JOURNAL OF ANATOMY (2014)

Article Clinical Neurology

Nutritional Practices at a Glance: Spinal Muscular Atrophy Type I Nutrition Survey Findings

Rebecca Hurst Davis et al.

JOURNAL OF CHILD NEUROLOGY (2014)

Article Multidisciplinary Sciences

SMN2 splicing modifiers improve motor function and longevity in mice with spinal muscular atrophy

Nikolai A. Naryshkin et al.

SCIENCE (2014)

Article Biochemistry & Molecular Biology

Severe SMA mice show organ impairment that cannot be rescued by therapy with the HDACi JNJ-26481585

Julia Schreml et al.

EUROPEAN JOURNAL OF HUMAN GENETICS (2013)

Article Biotechnology & Applied Microbiology

A Novel Morpholino Oligomer Targeting ISS-N1 Improves Rescue of Severe Spinal Muscular Atrophy Transgenic Mice

Haiyan Zhou et al.

HUMAN GENE THERAPY (2013)

Review Biochemistry & Molecular Biology

Spinal muscular atrophy: going beyond the motor neuron

Gillian Hamilton et al.

TRENDS IN MOLECULAR MEDICINE (2013)

Article Biochemistry & Molecular Biology

A single administration of morpholino antisense oligomer rescues spinal muscular atrophy in mouse

Paul N. Porensky et al.

HUMAN MOLECULAR GENETICS (2012)

Article Gastroenterology & Hepatology

Enteric Neuronal Density Contributes to the Severity of Intestinal Inflammation

Kara Gross Margolis et al.

GASTROENTEROLOGY (2011)

Article Biochemistry & Molecular Biology

Intravenous scAAV9 delivery of a codon-optimized SMN1 sequence rescues SMA mice

Elisa Dominguez et al.

HUMAN MOLECULAR GENETICS (2011)

Article Biochemistry & Molecular Biology

Design principles for bifunctional targeted oligonucleotide enhancers of splicing

Nicholas Owen et al.

NUCLEIC ACIDS RESEARCH (2011)

Article Biochemistry & Molecular Biology

Cardiac defects contribute to the pathology of spinal muscular atrophy models

Monir Shababi et al.

HUMAN MOLECULAR GENETICS (2010)

Article Medicine, Research & Experimental

CNS-targeted gene therapy improves survival and motor function in a mouse model of spinal muscular atrophy

Marco A. Passini et al.

JOURNAL OF CLINICAL INVESTIGATION (2010)

Article Clinical Neurology

DIGITAL NECROSES AND VASCULAR THROMBOSIS IN SEVERE SPINAL MUSCULAR ATROPHY

Sabine Rudnik-Schoeneborn et al.

MUSCLE & NERVE (2010)

Article Biotechnology & Applied Microbiology

Rescue of the spinal muscular atrophy phenotype in a mouse model by early postnatal delivery of SMN

Kevin D. Foust et al.

NATURE BIOTECHNOLOGY (2010)

Article Cell Biology

Systemic Delivery of scAAV9 Expressing SMN Prolongs Survival in a Model of Spinal Muscular Atrophy

Chiara F. Valori et al.

SCIENCE TRANSLATIONAL MEDICINE (2010)

Article Pediatrics

Vascular Perfusion Abnormalities in Infants with Spinal Muscular Atrophy

Alexandra Prufer de Queiroz Campos Araujo et al.

JOURNAL OF PEDIATRICS (2009)

Article Radiology, Nuclear Medicine & Medical Imaging

Chronic Mesenteric Ischemia: Diagnosis and Treatment

Eric Hohenwalter

SEMINARS IN INTERVENTIONAL RADIOLOGY (2009)

Article Gastroenterology & Hepatology

Enteric nervous system abnormalities in inflammatory bowel diseases

V. Villanacci et al.

NEUROGASTROENTEROLOGY AND MOTILITY (2008)

Article Clinical Neurology

Consensus statement for Standard of Care in Spinal Muscular Atrophy

Ching H. Wang et al.

JOURNAL OF CHILD NEUROLOGY (2007)

Article Genetics & Heredity

A mouse model for spinal muscular atrophy

HM Hsieh-Li et al.

NATURE GENETICS (2000)