4.5 Article

Disease burden of spinal muscular atrophy in Germany

Related references

Note: Only part of the references are listed.
Article Clinical Neurology

Developing therapies for spinal muscular atrophy

Mary H. Wertz et al.

SPECIAL ISSUE: THE YEAR IN NEUROLOGY AND PSYCHIATRY (2016)

Review Clinical Neurology

Spinal muscular atrophy-recent therapeutic advances for an old challenge

Irene Faravelli et al.

NATURE REVIEWS NEUROLOGY (2015)

Article Clinical Neurology

Spinal Muscular Atrophy

Stephen J. Kolb et al.

NEUROLOGIC CLINICS (2015)

Article Pediatrics

Spinal Muscular Atrophies

Basil T. Darras

PEDIATRIC CLINICS OF NORTH AMERICA (2015)

Article Clinical Neurology

COST OF ILLNESS FOR NEUROMUSCULAR DISEASES IN THE UNITED STATES

Jane Larkindale et al.

MUSCLE & NERVE (2014)

Article Clinical Neurology

The burden of Duchenne muscular dystrophy An international, cross-sectional study

Erik Landfeldt et al.

NEUROLOGY (2014)

Article Genetics & Heredity

Comparative cost of illness analysis and assessment of health care burden of Duchenne and Becker muscular dystrophies in Germany

Olivia Schreiber-Katz et al.

ORPHANET JOURNAL OF RARE DISEASES (2014)

Editorial Material Medicine, General & Internal

Patient reported outcome measures could help transform healthcare

Nick Black

BMJ-BRITISH MEDICAL JOURNAL (2013)

Article Clinical Neurology

Prospective cohort study of spinal muscular atrophy types 2 and 3

Petra Kaufmann et al.

NEUROLOGY (2012)

Article Clinical Neurology

Self-reported quality of life has no correlation with functional status in children and adolescents with spinal muscular atrophy

Cristiane M. de Oliveira et al.

EUROPEAN JOURNAL OF PAEDIATRIC NEUROLOGY (2011)

Review Genetics & Heredity

Spinal muscular atrophy

Adele D'Amico et al.

ORPHANET JOURNAL OF RARE DISEASES (2011)

Review Public, Environmental & Occupational Health

Economic analysis based on multinational studies: methods for adapting findings to national contexts

Thomas Reinhold et al.

JOURNAL OF PUBLIC HEALTH-HEIDELBERG (2010)

Article Clinical Neurology

Survival in SMA type I: A prospective analysis of 34 consecutive cases

J. M. Cobben et al.

NEUROMUSCULAR DISORDERS (2008)

Article Medicine, General & Internal

Exploration of the value of health-related quality-of-life information from clinical research and into clinical practice

Gordon H. Guyatt et al.

MAYO CLINIC PROCEEDINGS (2007)

Article Clinical Neurology

Consensus statement for Standard of Care in Spinal Muscular Atrophy

Ching H. Wang et al.

JOURNAL OF CHILD NEUROLOGY (2007)

Article Clinical Neurology

Reliability of 4 outcome measures in pediatric spinal muscular atrophy

ST Iannaccone et al.

ARCHIVES OF NEUROLOGY (2003)

Article Clinical Neurology

Outcome measures for pediatric spinal muscular atrophy

ST Iannaccone

ARCHIVES OF NEUROLOGY (2002)