Related references
Note: Only part of the references are listed.mRNA Vaccines in the COVID-19 Pandemic and Beyond
Michael J. Hogan et al.
ANNUAL REVIEW OF MEDICINE (2022)
Engineered virus-like particles for efficient in vivo delivery of therapeutic proteins
Samagya Banskota et al.
CELL (2022)
A flexible split prime editor using truncated reverse transcriptase improves dual-AAV delivery in mouse liver
Chunwei Zheng et al.
MOLECULAR THERAPY (2022)
Prime editing efficiency and fidelity are enhanced in the absence of mismatch repair
J. Ferreira da Silva et al.
NATURE COMMUNICATIONS (2022)
Dual-AAV delivering split prime editor system for in vivo genome editing
Shengyao Zhi et al.
MOLECULAR THERAPY (2022)
An engineered prime editor with enhanced editing efficiency in plants
Yuan Zong et al.
NATURE BIOTECHNOLOGY (2022)
Highly efficient prime editing by introducing same-sense mutations in pegRNA or stabilizing its structure
Xiaosa Li et al.
NATURE COMMUNICATIONS (2022)
PEAR, a flexible fluorescent reporter for the identification and enrichment of successfully prime edited cells
Dorottya Anna Simon et al.
ELIFE (2022)
HDAC inhibitors improve CRISPR-Cas9 mediated prime editing and base editing
Nan Liu et al.
MOLECULAR THERAPY-NUCLEIC ACIDS (2022)
Application of prime editing to the correction of mutations and phenotypes in adult mice with liver and eye diseases
Hyewon Jang et al.
NATURE BIOMEDICAL ENGINEERING (2022)
Expansion of the prime editing modality with Cas9 from Francisella novicida
Yeounsun Oh et al.
GENOME BIOLOGY (2022)
Ionization and structural properties of mRNA lipid nanoparticles influence expression in intramuscular and intravascular administration
Manuel J. Carrasco et al.
COMMUNICATIONS BIOLOGY (2021)
Precise genome engineering in Drosophila using prime editing
Justin A. Bosch et al.
PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA (2021)
Broadening the reach and investigating the potential of prime editors through fully viral gene-deleted adenoviral vector delivery
Qian Wang et al.
NUCLEIC ACIDS RESEARCH (2021)
A novel mechanism for the loss of mRNA activity in lipid nanoparticle delivery systems
Meredith Packer et al.
NATURE COMMUNICATIONS (2021)
Encapsulation state of messenger RNA inside lipid nanoparticles
Mark L. Brader et al.
BIOPHYSICAL JOURNAL (2021)
In vivo CRISPR base editing of PCSK9 durably lowers cholesterol in primates
Kiran Musunuru et al.
NATURE (2021)
Genome-wide specificity of prime editors in plants
Shuai Jin et al.
NATURE BIOTECHNOLOGY (2021)
Improved prime editors enable pathogenic allele correction and cancer modelling in adult mice
Pengpeng Liu et al.
NATURE COMMUNICATIONS (2021)
Nucleic acid delivery for therapeutic applications
Akash Gupta et al.
ADVANCED DRUG DELIVERY REVIEWS (2021)
CRISPR-Cas9 In Vivo Gene Editing for Transthyretin Amyloidosis
Julian D. Gillmore et al.
NEW ENGLAND JOURNAL OF MEDICINE (2021)
Efficient and precise generation of Tay-Sachs disease model in rabbit by prime editing system
Yuqiang Qian et al.
CELL DISCOVERY (2021)
Illuminating endosomal escape of polymorphic lipid nanoparticles that boost mRNA delivery
Marco Herrera et al.
BIOMATERIALS SCIENCE (2021)
CRISPR TREATMENT INSERTED DIRECTLY INTO BODY FOR THE FIRST TIME
Heidi Ledford
NATURE (2020)
Imaging small molecule-induced endosomal escape of siRNA
Hampus Du Rietz et al.
NATURE COMMUNICATIONS (2020)
Deconvoluting Lipid Nanoparticle Structure for Messenger RNA Delivery
Yulia Eygeris et al.
NANO LETTERS (2020)
Efficient generation of mouse models with the prime editing system
Yao Liu et al.
CELL DISCOVERY (2020)
Genome editing with CRISPR-Cas nucleases, base editors, transposases and prime editors
Andrew V. Anzalone et al.
NATURE BIOTECHNOLOGY (2020)
Unbiased investigation of specificities of prime editing systems in human cells
Do Yon Kim et al.
NUCLEIC ACIDS RESEARCH (2020)
Prime editing for functional repair in patient-derived disease models
Imre F. Schene et al.
NATURE COMMUNICATIONS (2020)
Corrector therapies (with or without potentiators) for people with cystic fibrosis with class II CFTR gene variants (most commonly F508del)
Kevin W. Southern et al.
COCHRANE DATABASE OF SYSTEMATIC REVIEWS (2020)
Non-Viral Delivery To Enable Genome Editing
Yuan Rui et al.
TRENDS IN BIOTECHNOLOGY (2019)
Search-and-replace genome editing without double-strand breaks or donor DNA
Andrew V. Anzalone et al.
NATURE (2019)
Brief update on endocytosis of nanomedicines
Siddharth Patel et al.
ADVANCED DRUG DELIVERY REVIEWS (2019)
Successful reprogramming of cellular protein production through mRNA delivered by functionalized lipid nanoparticles
Marianna Yanez Arteta et al.
PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA (2018)
The Promise and Challenge of In Vivo Delivery for Genome Therapeutics
Ross C. Wilson et al.
ACS CHEMICAL BIOLOGY (2018)
Programmable base editing of A.T to G.C in genomic DNA without DNA cleavage
Nicole M. Gaudelli et al.
NATURE (2017)
Structure-guided chemical modification of guide RNA enables potent non-viral in vivo genome editing
Hao Yin et al.
NATURE BIOTECHNOLOGY (2017)
Characterizing exogenous mRNA delivery, trafficking, cytoplasmic release and RNA-protein correlations at the level of single cells
Jonathan L. Kirschman et al.
NUCLEIC ACIDS RESEARCH (2017)
ClinVar: public archive of interpretations of clinically relevant variants
Melissa J. Landrum et al.
NUCLEIC ACIDS RESEARCH (2016)
Microfluidic Mixing: A General Method for Encapsulating Macromolecules in Lipid Nanoparticle Systems
Alex K. K. Leung et al.
JOURNAL OF PHYSICAL CHEMISTRY B (2015)
A Programmable Dual-RNA-Guided DNA Endonuclease in Adaptive Bacterial Immunity
Martin Jinek et al.
SCIENCE (2012)