Related references
Note: Only part of the references are listed.GPR108 Is a Highly Conserved AAV Entry Factor
Amanda M. Dudek et al.
MOLECULAR THERAPY (2020)
Structure comparison of the chimeric AAV2.7m8 vector with parental AAV2
Antonette Bennett et al.
JOURNAL OF STRUCTURAL BIOLOGY (2020)
Management of Neuroinflammatory Responses to AAV-Mediated Gene Therapies for Neurodegenerative Diseases
Barbara A. Perez et al.
BRAIN SCIENCES (2020)
Suprachoroidal and Subretinal Injections of AAV Using Transscleral Microneedles for Retinal Gene Delivery in Nonhuman Primates
Glenn Yiu et al.
MOLECULAR THERAPY-METHODS & CLINICAL DEVELOPMENT (2020)
Novel AAV44.9-Based Vectors Display Exceptional Characteristics for Retinal Gene Therapy
Sanford L. Boye et al.
MOLECULAR THERAPY (2020)
Luxturna: FDA documents reveal the value of a costly gene therapy
Jonathan J. Darrow
DRUG DISCOVERY TODAY (2019)
Adeno-Associated Virus (AAV) Versus Immune Response
Joseph Rabinowitz et al.
VIRUSES-BASEL (2019)
Polarized AAVR expression determines infectivity by AAV gene therapy vectors
Bradley A. Hamilton et al.
GENE THERAPY (2019)
Recombinant Adeno-Associated Virus Gene Therapy in Light of Luxturna (and Zolgensma and Glybera): Where Are We, and How Did We Get Here?
Allison M. Keeler et al.
ANNUAL REVIEW OF VIROLOGY, VOL 6, 2019 (2019)
AAV8-vectored suprachoroidal gene transfer produces widespread ocular transgene expression
Kun Ding et al.
JOURNAL OF CLINICAL INVESTIGATION (2019)
Comprehensive AAV capsid fitness landscape reveals a viral gene and enables machine-guided design
Pierce J. Ogden et al.
SCIENCE (2019)
Retinal explant culture: A platform to investigate human neuro-retina
Aparna Murali et al.
CLINICAL AND EXPERIMENTAL OPHTHALMOLOGY (2019)
Evaluation of AAV-DJ vector for retinal gene therapy
Yusaku Katada et al.
PEERJ (2019)
Vector uncoating limits adenoassociated viral vector-mediated transduction of human dendritic cells and vector immunogenicity
Axel Rossi et al.
SCIENTIFIC REPORTS (2019)
Light and the laboratory mouse
Stuart N. Peirson et al.
JOURNAL OF NEUROSCIENCE METHODS (2018)
The Neurotropic Properties of AAV-PHP.B Are Limited to C57BL/6J Mice
Juliette Hordeaux et al.
MOLECULAR THERAPY (2018)
Seeing the Light after 25 Years of Retinal Gene Therapy
Ivana Trapani et al.
TRENDS IN MOLECULAR MEDICINE (2018)
Volumetric Measurement of Subretinal Blebs Using Microscope-Integrated Optical Coherence Tomography
S. Tammy Hsu et al.
TRANSLATIONAL VISION SCIENCE & TECHNOLOGY (2018)
Deamidation of Amino Acids on the Surface of Adeno-Associated Virus Capsids Leads to Charge Heterogeneity and Altered Vector Function
April R. Giles et al.
MOLECULAR THERAPY (2018)
Humoral Immune Response After Intravitreal But Not After Subretinal AAV8 in Primates and Patients
Felix F. Reichel et al.
INVESTIGATIVE OPHTHALMOLOGY & VISUAL SCIENCE (2018)
Noninvasive gene delivery to foveal cones for vision restoration
Hanen Khabou et al.
JCI INSIGHT (2018)
The Future Looks Brighter After 25 Years of Retinal Gene Therapy
Alberto Auricchio et al.
HUMAN GENE THERAPY (2017)
AAV: An Overview of Unanswered Questions
Kenneth I. Berns et al.
HUMAN GENE THERAPY (2017)
Small But Increasingly Mighty: Latest Advances in AAV Vector Research, Design, and Evolution
Dirk Grimm et al.
HUMAN GENE THERAPY (2017)
Photoreceptor-targeted gene delivery using intravitreally administered AAV vectors in dogs (vol 23, pg 223, 2016)
R. F. Boyd et al.
GENE THERAPY (2016)
Reduced retinal transduction and enhanced transgene-directed immunogenicity with intravitreal delivery of rAAV following posterior vitrectomy in dogs
R. F. Boyd et al.
GENE THERAPY (2016)
Loss of HCN1 enhances disease progression in mouse models of CNG channel-linked retinitis pigmentosa and achromatopsia
Christian Schoen et al.
HUMAN MOLECULAR GENETICS (2016)
Heparan Sulfate Binding Promotes Accumulation of Intravitreally Delivered Adeno-associated Viral Vectors at the Retina for Enhanced Transduction but Weakly Influences Tropism
Kenton T. Woodard et al.
JOURNAL OF VIROLOGY (2016)
AAVR: A Multi-Serotype Receptor for AAV
Candace Summerford et al.
MOLECULAR THERAPY (2016)
AAV Vectors for FRET-Based Analysis of Protein-Protein Interactions in Photoreceptor Outer Segments
Elvir Becirovic et al.
FRONTIERS IN NEUROSCIENCE (2016)
Long-Term Effect of Gene Therapy on Leber's Congenital Amaurosis
J. W. B. Bainbridge et al.
NEW ENGLAND JOURNAL OF MEDICINE (2015)
Improvement and Decline in Vision with Gene Therapy in Childhood Blindness
Samuel G. Jacobson et al.
NEW ENGLAND JOURNAL OF MEDICINE (2015)
In Silico Reconstruction of the Viral Evolutionary Lineage Yields a Potent Gene Therapy Vector
Eric Zinn et al.
CELL REPORTS (2015)
Antibody neutralization poses a barrier to intravitreal adeno-associated viral vector gene delivery to non-human primates
M. A. Kotterman et al.
GENE THERAPY (2015)
Quick and reliable method for retina dissociation and separation of rod photoreceptor perikarya from adult mice
Yana Feodorova et al.
METHODSX (2015)
Tyrosine capsid-mutant AAV vectors for gene delivery to the canine retina from a subretinal or intravitreal approach
F. M. Mowat et al.
GENE THERAPY (2014)
Tropism-modified AAV Vectors Overcome Barriers to Successful Cutaneous Therapy
Jessica Sallach et al.
MOLECULAR THERAPY (2014)
Biophysical and Ultrastructural Characterization of Adeno-Associated Virus Capsid Uncoating and Genome Release
Eric D. Horowitz et al.
JOURNAL OF VIROLOGY (2013)
Human retinal gene therapy for Leber congenital amaurosis shows advancing retinal degeneration despite enduring visual improvement
Artur V. Cideciyan et al.
PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA (2013)
In Vivo-Directed Evolution of a New Adeno-Associated Virus for Therapeutic Outer Retinal Gene Delivery from the Vitreous
Deniz Dalkara et al.
SCIENCE TRANSLATIONAL MEDICINE (2013)
High-Resolution Comparative Modeling with RosettaCM
Yifan Song et al.
STRUCTURE (2013)
Gene therapy for retinal disease
Michelle E. McClements et al.
TRANSLATIONAL RESEARCH (2013)
Successful target cell transduction of capsid-engineered rAAV vectors requires clathrin-dependent endocytosis
S. Uhrig et al.
GENE THERAPY (2012)
Increased Integration of Transplanted CD73-Positive Photoreceptor Precursors into Adult Mouse Retina
Dominic Eberle et al.
INVESTIGATIVE OPHTHALMOLOGY & VISUAL SCIENCE (2011)
Improvement of Visual Performance With Intravitreal Administration of 9-cis-Retinal in Rpe65-Mutant Dogs
Patricia M. Gearhart et al.
ARCHIVES OF OPHTHALMOLOGY (2010)
Restoration of Cone Vision in the CNGA3-/- Mouse Model of Congenital Complete Lack of Cone Photoreceptor Function
Stylianos Michalakis et al.
MOLECULAR THERAPY (2010)
High-efficiency Transduction of the Mouse Retina by Tyrosine-mutant AAV Serotype Vectors
Hilda Petrs-Silva et al.
MOLECULAR THERAPY (2009)
Inner Limiting Membrane Barriers to AAV-mediated Retinal Transduction From the Vitreous
Deniz Dalkara et al.
MOLECULAR THERAPY (2009)
Structure prediction for CASP8 with all-atom refinement using Rosetta
Srivatsan Raman et al.
PROTEINS-STRUCTURE FUNCTION AND BIOINFORMATICS (2009)
Treatment of Leber Congenital Amaurosis Due to RPE65 Mutations by Ocular Subretinal Injection of Adeno-Associated Virus Gene Vector: Short-Term Results of a Phase I Trial
William W. Hauswirth et al.
HUMAN GENE THERAPY (2008)
Safety and efficacy of gene transfer for Leber's congenital amaurosis
Albert M. Maguire et al.
NEW ENGLAND JOURNAL OF MEDICINE (2008)
Effect of gene therapy on visual function in Leber's congenital amaurosis
James W. B. Bainbridge et al.
NEW ENGLAND JOURNAL OF MEDICINE (2008)
Heparan sulfate proteoglycan binding properties of adeno-associated virus retargeting mutants and consequences for their in vivo tropism
Luca Perabo et al.
JOURNAL OF VIROLOGY (2006)
Combinatorial engineering of a gene therapy vector:: directed evolution of adeno-associated virus
L Perabo et al.
JOURNAL OF GENE MEDICINE (2006)
Adeno-associated virus serotypes 1 to 5 mediated tumor cell directed gene transfer and improvement of transduction efficiency
UT Hacker et al.
JOURNAL OF GENE MEDICINE (2005)
Intracellular trafficking of adeno-associated viral vectors
W Ding et al.
GENE THERAPY (2005)
Impaired opsin targeting and cone photoreceptor migration in the retina of mice lacking the cyclic nucleotide-gated channel CNGA3
S Michalakis et al.
INVESTIGATIVE OPHTHALMOLOGY & VISUAL SCIENCE (2005)
UCSF chimera - A visualization system for exploratory research and analysis
EF Pettersen et al.
JOURNAL OF COMPUTATIONAL CHEMISTRY (2004)
Identification of a heparin-binding motif on adeno-associated virus type 2 capsids
A Kern et al.
JOURNAL OF VIROLOGY (2003)
In vitro selection of viral vectors with modified tropism:: The adeno-associated virus display
L Perabo et al.
MOLECULAR THERAPY (2003)
Identification of amino acid residues in the capsid proteins of adeno-associated virus type 2 that contribute to heparan sulfate proteoglycan binding
SR Opie et al.
JOURNAL OF VIROLOGY (2003)
Efficient and selective AAV2-mediated gene transfer directed to human vascular endothelial cells
SA Nicklin et al.
MOLECULAR THERAPY (2001)
Transgenic expression of the jellyfish green fluorescent protein in the cone photoreceptors of the mouse
YJ Fei et al.
VISUAL NEUROSCIENCE (2001)