Journal
EXPERT OPINION ON BIOLOGICAL THERAPY
Volume 20, Issue 10, Pages 1121-1124Publisher
TAYLOR & FRANCIS LTD
DOI: 10.1080/14712598.2020.1792880
Keywords
Huntington disease; huntingtin lowering; HTT; antisense oligonucleotide; ASO; adeno-associated virus; AAV5; microRNA
Funding
- uniQure biopharma B.V.