Journal
CIRCULATION
Volume 134, Issue 11, Pages 777-779Publisher
LIPPINCOTT WILLIAMS & WILKINS
DOI: 10.1161/CIRCULATIONAHA.116.024007
Keywords
adeno-associated virus; CRISPR; gene therapy; genome; muscular dystrophy, duchenne
Funding
- NHLBI NIH HHS [K08 HL094699] Funding Source: Medline