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LG Gregory et al.
MOLECULAR THERAPY (2003)
Evidence of CFTR function in cystic fibrosis after systemic administration of 4-phenylbutyrate
PL Zeitlin et al.
MOLECULAR THERAPY (2002)
Nucleoside triphosphate pentose ring impact on CFTR gating and hydrolysis
AA Aleksandrov et al.
FEBS LETTERS (2002)
A principal role for the proteasome in endoplasmic reticulum-associated degradation of misfolded intracellular cystic fibrosis transmembrane conductance regulator
MS Gelman et al.
JOURNAL OF BIOLOGICAL CHEMISTRY (2002)
Safety of local delivery of low- and intermediate-dose adenovirus gene transfer vectors to individuals with a spectrum of morbid conditions
BG Harvey et al.
HUMAN GENE THERAPY (2002)
Aerosol and lobar administration of a recombinant adenovirus to individuals with cystic fibrosis. I. Methods, safety, and clinical implications
PM Joseph et al.
HUMAN GENE THERAPY (2001)
Sodium 4-phenylbutyrate downregulates Hsc70:: implications for intracellular trafficking of ΔF508-CFTR
RC Rubenstein et al.
AMERICAN JOURNAL OF PHYSIOLOGY-CELL PHYSIOLOGY (2000)
A pilot study of the effect of gentamicin on nasal potential difference measurements in cystic fibrosis patients carrying stop mutations
M Wilschanski et al.
AMERICAN JOURNAL OF RESPIRATORY AND CRITICAL CARE MEDICINE (2000)