Related references
Note: Only part of the references are listed.Transfusion independence and HMGA2 activation after gene therapy of human β-thalassaemia
Marina Cavazzana-Calvo et al.
NATURE (2010)
Human hematopoietic stem/progenitor cells modified by zinc-finger nucleases targeted to CCR5 control HIV-1 in vivo
Nathalia Holt et al.
NATURE BIOTECHNOLOGY (2010)
Genomic instability and myelodysplasia with monosomy 7 consequent to EVI1 activation after gene therapy for chronic granulomatous disease
Stefan Stein et al.
NATURE MEDICINE (2010)
Deciphering the Code for Retroviral Integration Target Site Selection
Federico Andrea Santoni et al.
PLOS COMPUTATIONAL BIOLOGY (2010)
The genotoxic potential of retroviral vectors is strongly modulated by vector design and integration site selection in a mouse model of HSC gene therapy
Eugenio Montini et al.
JOURNAL OF CLINICAL INVESTIGATION (2009)
Stem Cell Marking With Promotor-deprived Self-inactivating Retroviral Vectors Does Not Lead to Induced Clonal Imbalance
Kerstin Cornils et al.
MOLECULAR THERAPY (2009)
Cell-intrinsic and Vector-related Properties Cooperate to Determine the Incidence and Consequences of Insertional Mutagenesis
Olga S. Kustikova et al.
MOLECULAR THERAPY (2009)
Molecular evolution of a novel hyperactive Sleeping Beauty transposase enables robust stable gene transfer in vertebrates
Lajos Mates et al.
NATURE GENETICS (2009)
Phase 2 gene therapy trial of an anti-HIV ribozyme in autologous CD34+ cells
Ronald T. Mitsuyasu et al.
NATURE MEDICINE (2009)
Long-Term Control of HIV by CCR5 Delta32/Delta32 Stem-Cell Transplantaion
Gero Huetter et al.
NEW ENGLAND JOURNAL OF MEDICINE (2009)
Gene Therapy for Immunodeficiency Due to Adenosine Deaminase Deficiency.
Alessandro Aiuti et al.
NEW ENGLAND JOURNAL OF MEDICINE (2009)
Protection of Stem Cell-Derived Lymphocytes in a Primate AIDS Gene Therapy Model after In Vivo Selection
Grant D. Trobridge et al.
PLOS ONE (2009)
Molecular control of HIV-1 postintegration latency: implications for the development of new therapeutic strategies
Laurence Colin et al.
RETROVIROLOGY (2009)
Resistance of mature T cells to oncogene transformation
Sebastian Newrzela et al.
BLOOD (2008)
Physiological promoters reduce the genotoxic risk of integrating gene vectors
Daniela Zychlinski et al.
MOLECULAR THERAPY (2008)
Establishment of HIV-1 resistance in CD4+ T cells by genome editing using zinc-finger nucleases
Elena E. Perez et al.
NATURE BIOTECHNOLOGY (2008)
Low-level viremia persists for at least 7 years in patients on suppressive antiretroviral therapy
Sarah Palmer et al.
PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA (2008)
Insertional mutagenesis and clonal dominance: biological and statistical considerations
B. Fehse et al.
GENE THERAPY (2008)
Semen-derived amyloid fibrils drastically enhance HIV infection
Jan Muench et al.
CELL (2007)
Genetic therapies against HIV
John J. Rossi et al.
NATURE BIOTECHNOLOGY (2007)
Targeted genome modifications using integrase-deficient lentiviral vectors
Tatjana I. Cornu et al.
MOLECULAR THERAPY (2007)
Antiretroviral therapy with the integrase inhibitor raltegravir alters decay kinetics of HIV, significantly reducing the second phase
John M. Murray et al.
AIDS (2007)
Gene editing in human stem cells using zinc finger nucleases and integrase-defective lentiviral vector delivery
Angelo Lombardo et al.
NATURE BIOTECHNOLOGY (2007)
HIV-1 proviral DNA excision using an evolved recombinase
Indrani Sarkar et al.
SCIENCE (2007)
Microbial translocation is a cause of systemic immune activation in chronic HIV infection
Jason M. Brenchley et al.
NATURE MEDICINE (2006)
Cell-culture assays reveal the importance of retroviral vector design for insertional genotoxicity
Ute Modlich et al.
BLOOD (2006)
Cancer regression in patients after transfer of genetically engineered lymphocytes
Richard A. Morgan et al.
SCIENCE (2006)
Hematopoietic stem cell gene transfer in a tumor-prone mouse model uncovers low genotoxicity of lentiviral vector integration
Eugenio Montini et al.
NATURE BIOTECHNOLOGY (2006)
Impact of gene-modified T cells on HIV infection dynamics
D von Laer et al.
JOURNAL OF THEORETICAL BIOLOGY (2006)
Gene therapy for HIV infection: what does it need to make it work?
Dorothee von Laer et al.
JOURNAL OF GENE MEDICINE (2006)
Retroviral DNA integration: ASLV, HIV, and MLV show distinct target site preferences
RS Mitchell et al.
PLOS BIOLOGY (2004)
Talking about a revolution: The impact of site-specific recombinases on genetic analyses in mice
CS Branda et al.
DEVELOPMENTAL CELL (2004)
Side effects of retroviral gene transfer into hematopoietic stem cells
C Baum et al.
BLOOD (2003)
Dose finding with retroviral vectors: correlation of retroviral vector copy numbers in single cells with gene transfer efficiency in a cell population
OS Kustikova et al.
BLOOD (2003)
Conditional control of gene expression in the mouse
M Lewandoski
NATURE REVIEWS GENETICS (2001)