3.9 Article

A Capillary Electrophoresis Sequencing Method for the Identification of Mutations in the Inverted Terminal Repeats of Adeno-Associated Virus

Related references

Note: Only part of the references are listed.
Review Biotechnology & Applied Microbiology

The AAV Vector Toolkit: Poised at the Clinical Crossroads

Aravind Asokan et al.

MOLECULAR THERAPY (2012)

Review Genetics & Heredity

Therapeutic in vivo gene transfer for genetic disease using AAV: progress and challenges

Federico Mingozzi et al.

NATURE REVIEWS GENETICS (2011)

Article Medicine, General & Internal

Adenovirus-Associated Virus Vector-Mediated Gene Transfer in Hemophilia B

Amit C. Nathwani et al.

NEW ENGLAND JOURNAL OF MEDICINE (2011)

Article Biotechnology & Applied Microbiology

Gene Therapy for Leber's Congenital Amaurosis is Safe and Effective Through 1.5 Years After Vector Administration

Francesca Simonelli et al.

MOLECULAR THERAPY (2010)

Review Microbiology

Gene Therapy Using Adeno-Associated Virus Vectors

Shyam Daya et al.

CLINICAL MICROBIOLOGY REVIEWS (2008)

Article Medicine, General & Internal

Safety and efficacy of gene transfer for Leber's congenital amaurosis

Albert M. Maguire et al.

NEW ENGLAND JOURNAL OF MEDICINE (2008)

Article Medicine, General & Internal

Effect of gene therapy on visual function in Leber's congenital amaurosis

James W. B. Bainbridge et al.

NEW ENGLAND JOURNAL OF MEDICINE (2008)

Article Multidisciplinary Sciences

Human gene therapy for RPE65 isomerase deficiency activates the retinoid cycle of vision but with slow rod kinetics

Artur V. Cideciyan et al.

PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA (2008)

Article Multidisciplinary Sciences

Modulation of metabolic brain networks after subthalamic gene therapy for Parkinson's disease

Andrew Feigin et al.

PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA (2007)