Related references
Note: Only part of the references are listed.
Review
Genetics & Heredity
Pricing and reimbursement of orphan drugs: the need for more transparency
Steven Simoens
ORPHANET JOURNAL OF RARE DISEASES (2011)
Article
Economics
Drugs for Rare Diseases: Influence of Orphan Designation Status on Price
Eline Picavet et al.
APPLIED HEALTH ECONOMICS AND HEALTH POLICY (2011)
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Are rare diseases still orphans or happily adopted? The challenges of developing and using orphan medicinal products
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BRITISH JOURNAL OF CLINICAL PHARMACOLOGY (2006)