Related references
Note: Only part of the references are listed.Rationally engineered Cas9 nucleases with improved specificity
Ian M. Slaymaker et al.
SCIENCE (2016)
Postnatal genome editing partially restores dystrophin expression in a mouse model of muscular dystrophy
Chengzu Long et al.
SCIENCE (2016)
In vivo gene editing in dystrophic mouse muscle and muscle stem cells
Mohammadsharif Tabebordbar et al.
SCIENCE (2016)
In vivo genome editing improves muscle function in a mouse model of Duchenne muscular dystrophy
Christopher E. Nelson et al.
SCIENCE (2016)
CRISPR/Cas9 in Genome Editing and Beyond
Haifeng Wang et al.
ANNUAL REVIEW OF BIOCHEMISTRY, VOL 85 (2016)
Co-expression of phenylalanine hydroxylase variants and effects of interallelic complementation on in vitro enzyme activity and genotype-phenotype correlation
Nan Shen et al.
MOLECULAR GENETICS AND METABOLISM (2016)
RS-1 enhances CRISPR/Cas9-and TALEN-mediated knock-in efficiency
Jun Song et al.
NATURE COMMUNICATIONS (2016)
Precision Medicine: Genetic Repair of Retinitis Pigmentosa in Patient-Derived Stem Cells
Alexander G. Bassuk et al.
SCIENTIFIC REPORTS (2016)
Increasing the efficiency of precise genome editing with CRISPR-Cas9 by inhibition of nonhomologous end joining
Takeshi Maruyama et al.
NATURE BIOTECHNOLOGY (2015)
Nuclear domain 'knock-in' screen for the evaluation and identification of small molecule enhancers of CRISPR-based genome editing
Jordan Pinder et al.
NUCLEIC ACIDS RESEARCH (2015)
Efficient fdCas9 Synthetic Endonuclease with Improved Specificity for Precise Genome Engineering
Mustapha Aouida et al.
PLOS ONE (2015)
Generation of mutant mice via the CRISPR/Cas9 system using FokI-dCas9
Satoshi Hara et al.
SCIENTIFIC REPORTS (2015)
CasOT: a genome-wide Cas9/gRNA off-target searching tool
An Xiao et al.
BIOINFORMATICS (2014)
Development and Applications of CRISPR-Cas9 for Genome Engineering
Patrick D. Hsu et al.
CELL (2014)
Molecular genetics and diagnosis of phenylketonuria: state of the art
Nenad Blau et al.
EXPERT REVIEW OF MOLECULAR DIAGNOSTICS (2014)
Seamless gene correction of β-thalassemia mutations in patient-specific iPSCs using CRISPR/Cas9 and piggyBac
Fei Xie et al.
GENOME RESEARCH (2014)
Dimeric CRISPR RNA-guided Fokl nucleases for highly specific genome editing
Shengdar Q. Tsai et al.
NATURE BIOTECHNOLOGY (2014)
CRISPR-Cas systems for editing, regulating and targeting genomes
Jeffry D. Sander et al.
NATURE BIOTECHNOLOGY (2014)
Genome-wide analysis reveals characteristics of off-target sites bound by the Cas9 endonuclease
Cem Kuscu et al.
NATURE BIOTECHNOLOGY (2014)
Fusion of catalytically inactive Cas9 to Fokl nuclease improves the specificity of genome modification
John P. Guilinger et al.
NATURE BIOTECHNOLOGY (2014)
Genome editing with Cas9 in adult mice corrects a disease mutation and phenotype
Hao Yin et al.
NATURE BIOTECHNOLOGY (2014)
Efficient genome modification by CRISPR-Cas9 nickase with minimal off-target effects
Bin Shen et al.
NATURE METHODS (2014)
E-CRISP: fast CRISPR target site identification
Florian Heigwer et al.
NATURE METHODS (2014)
New Strategies for the Treatment of Phenylketonuria (PKU)
Pietro Strisciuglio et al.
METABOLITES (2014)
Tetrahydrobiopterin, its Mode of Action on Phenylalanine Hydroxylase, and Importance of Genotypes for Pharmacological Therapy of Phenylketonuria
Caroline Heintz et al.
HUMAN MUTATION (2013)
High-frequency off-target mutagenesis induced by CRISPR-Cas nucleases in human cells
Yanfang Fu et al.
NATURE BIOTECHNOLOGY (2013)
Applications of the Restriction Free (RF) cloning procedure for molecular manipulations and protein expression
Tamar Unger et al.
JOURNAL OF STRUCTURAL BIOLOGY (2010)
Future treatment strategies in phenylketonuria
Francjan J. van Spronsen et al.
MOLECULAR GENETICS AND METABOLISM (2010)
A chemical compound that stimulates the human homologous recombination protein RAD51
Krishanthi Jayathilaka et al.
PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA (2008)
Share Paper
