4.1 Editorial Material

On the road to gene therapy for beta-thalassemia and sickle cell anemia

Journal

PEDIATRIC HEMATOLOGY AND ONCOLOGY
Volume 25, Issue 1, Pages 1-4

Publisher

TAYLOR & FRANCIS INC
DOI: 10.1080/08880010701773829

Keywords

human globin gene therapy; thalassemia; sickle cell disease

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Human globin gene therapy is a potential cure for sickle cell disease and beta-thalassemia (Cooley anemia). A clinical trial of this treatment is currently under way in Paris using lentiglobin vectors.

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