4.8 Article

Genome editing with Cas9 in adult mice corrects a disease mutation and phenotype

Related references

Note: Only part of the references are listed.
Article Biochemistry & Molecular Biology

Double Nicking by RNA-Guided CRISPR Cas9 for Enhanced Genome Editing Specificity

F. Ann Ran et al.

Article Cell & Tissue Engineering

Correction of a Genetic Disease in Mouse via Use of CRISPR-Cas9

Yuxuan Wu et al.

CELL STEM CELL (2013)

Article Biotechnology & Applied Microbiology

DNA targeting specificity of RNA-guided Cas9 nucleases

Patrick D. Hsu et al.

NATURE BIOTECHNOLOGY (2013)

Article Biotechnology & Applied Microbiology

Targeted genome engineering in human cells with the Cas9 RNA-guided endonuclease

Seung Woo Cho et al.

NATURE BIOTECHNOLOGY (2013)

Article Biotechnology & Applied Microbiology

High-frequency off-target mutagenesis induced by CRISPR-Cas nucleases in human cells

Yanfang Fu et al.

NATURE BIOTECHNOLOGY (2013)

Review Chemistry, Physical

Delivery materials for siRNA therapeutics

Rosemary Kanasty et al.

NATURE MATERIALS (2013)

Article Multidisciplinary Sciences

RNA-Guided Human Genome Engineering via Cas9

Prashant Mali et al.

SCIENCE (2013)

Article Multidisciplinary Sciences

Multiplex Genome Engineering Using CRISPR/Cas Systems

Le Cong et al.

SCIENCE (2013)

Article Multidisciplinary Sciences

In vivo genome editing restores haemostasis in a mouse model of haemophilia

Hojun Li et al.

NATURE (2011)

Article Gastroenterology & Hepatology

Adeno-Associated Virus Gene Repair Corrects a Mouse Model of Hereditary Tyrosinemia In Vivo

Nicole K. Paulk et al.

HEPATOLOGY (2010)

Article Biotechnology & Applied Microbiology

Robust expansion of human hepatocytes in Fah-/-/Rag2-/-/Il2rg-/- mice

Hisaya Azuma et al.

NATURE BIOTECHNOLOGY (2007)

Article Multidisciplinary Sciences

Point mutations in the murine fumarylacetoacetate hydrolase gene: Animal models for the human genetic disorder hereditary tyrosinemia type 1

JL Aponte et al.

PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA (2001)