4.5 Article

A fusion peptide directs enhanced systemic dystrophin exon skipping and functional restoration in dystrophin-deficient mdx mice

Related references

Note: Only part of the references are listed.
Article Biotechnology & Applied Microbiology

Sustained dystrophin expression induced by peptide-conjugated morpholino oligomers in the muscles of mdx mice

Natee Jearawiriyapaisarn et al.

MOLECULAR THERAPY (2008)

Article Multidisciplinary Sciences

Effective rescue of dystrophin improves cardiac function in dystrophin-deficient mice by a modified morpholino oligomer

Bo Wu et al.

PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA (2008)

Article Medicine, General & Internal

Local dystrophin restoration with antisense oligonucleotide PRO051

Judith C. van Deutekom et al.

NEW ENGLAND JOURNAL OF MEDICINE (2007)

Article Multidisciplinary Sciences

Transvascular delivery of small interfering RNA to the central nervous system

Priti Kumar et al.

NATURE (2007)

Article Biotechnology & Applied Microbiology

Antisense oligonucleotide-induced exon skipping across the human dystrophin gene transcript

Steve D. Wilton et al.

MOLECULAR THERAPY (2007)

Article Multidisciplinary Sciences

Systemic delivery of antisense oligoribonucleotide restores dystrophin expression in body-wide skeletal muscles

QL Lu et al.

PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA (2005)

Article Biochemistry & Molecular Biology

Systemic delivery of genes to striated muscles using adeno-associated viral vectors

P Gregorevic et al.

NATURE MEDICINE (2004)

Article Genetics & Heredity

Antisense-induced multiexon skipping for Duchenne muscular dystrophy makes more sense

A Aartsma-Rus et al.

AMERICAN JOURNAL OF HUMAN GENETICS (2004)

Article Biochemistry & Molecular Biology

Functional amounts of dystrophin produced by skipping the mutated exon in the mdx dystrophic mouse

QL Lu et al.

NATURE MEDICINE (2003)

Article Biochemistry & Molecular Biology

Morpholino antisense oligonucleotide induced dystrophin exon 23 skipping in mdx mouse muscle

BL Gebski et al.

HUMAN MOLECULAR GENETICS (2003)

Article Biochemistry & Molecular Biology

Therapeutic antisense-induced exon skipping in cultured muscle cells from six different DMD patients

A Aartsma-Rus et al.

HUMAN MOLECULAR GENETICS (2003)

Article Developmental Biology

Low grip strength, impaired tongue force and hyperactivity induced by overexpression of neurotrophin-3 in mouse skeletal muscle

SC Fowler et al.

INTERNATIONAL JOURNAL OF DEVELOPMENTAL NEUROSCIENCE (2002)

Review Physiology

Function and genetics of dystrophin and dystrophin-related proteins in muscle

DJ Blake et al.

PHYSIOLOGICAL REVIEWS (2002)