4.5 Article

Gene Therapy in Ophthalmology: Validation on Cultured Retinal Cells and Explants from Postmortem Human Eyes

Related references

Note: Only part of the references are listed.
Article Biochemistry & Molecular Biology

Gene therapy rescues cone function in congenital achromatopsia

Andras M. Komaromy et al.

HUMAN MOLECULAR GENETICS (2010)

Letter Medicine, General & Internal

Vision 1 Year after Gene Therapy for Leber's Congenital Amaurosis

Artur V. Cideciyan et al.

NEW ENGLAND JOURNAL OF MEDICINE (2009)

Editorial Material Biochemistry & Molecular Biology

Sucess in sight: The eyes have it! Ocular gene therapy trials for LCA look promising

J. W. Bainbridge et al.

GENE THERAPY (2008)

Article Medicine, General & Internal

Safety and efficacy of gene transfer for Leber's congenital amaurosis

Albert M. Maguire et al.

NEW ENGLAND JOURNAL OF MEDICINE (2008)

Article Medicine, General & Internal

Effect of gene therapy on visual function in Leber's congenital amaurosis

James W. B. Bainbridge et al.

NEW ENGLAND JOURNAL OF MEDICINE (2008)

Article Multidisciplinary Sciences

Human gene therapy for RPE65 isomerase deficiency activates the retinoid cycle of vision but with slow rod kinetics

Artur V. Cideciyan et al.

PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA (2008)

Article Biotechnology & Applied Microbiology

Safety in nonhuman primates of ocular AAV2-RPE65, a candidate treatment for blindness in leber congenital amaurosis

Samuel G. Jacobson et al.

HUMAN GENE THERAPY (2006)

Article Neurosciences

Excessive activation of cyclic nucleotide-gated channels contributes to neuronal degeneration of photoreceptors

G Vallazza-Deschamps et al.

EUROPEAN JOURNAL OF NEUROSCIENCE (2005)

Article Biotechnology & Applied Microbiology

In utero gene therapy rescues vision in a murine model of congenital blindness

NS Dejneka et al.

MOLECULAR THERAPY (2004)

Article Genetics & Heredity

Gene therapy restores vision in a canine model of childhood blindness

GM Acland et al.

NATURE GENETICS (2001)